日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Beyond Trikafta: new models to assess tissue dependent rescue of N1303K-CFTR

Trikafta 之外:评估 N1303K-CFTR 组织依赖性拯救的新模型

Pranke, Iwona; Capurro, Valeria; Chevalier, Benoit; Pesce, Emanuela; Tomati, Valeria; Pastorino, Cristina; Kelly-Aubert, Mairead; Hatton, Aurelie; Dreano, Elise; Lena, Mariateresa; Bocciardi, Renata; Zara, Federico; Pantano, Stefano; Terlizzi, Vito; Lucanto, Cristina; Costa, Stefano; Claut, Laura; Daccò, Valeria; Poli, Piercarlo; Maschio, Massimo; Fabrizzi, Benedetta; Caporelli, Nicole; Cipolli, Marco; Volpi, Sonia; Chedevergne, Frederique; Cosson, Laure; Macey, Julie; Ramel, Sophie; Weiss, Laurence; Grenet, Dominique; Le Clainche-Viala, Laurence; Douvry, Benoit; Ravoninjatovo, Bruno; Audousset, Camille; Tatopoulos, Aurélie; Richaud-Thiriez, Bénédicte; Baravalle, Melissa; Thouvenin, Guillaume; Labbé, Guillaume; Mittaine, Marie; Reix, Philippe; Durieu, Isabelle; Mankikian, Julie; Bui, Stéphanie; Nguyen-Khoa, Thao; Khoukh, Karim; Martin, Clémence; Da Silva, Jennifer; De Carli, Paola; Castellani, Carlo; Cresta, Federico; Galietta, Luis; Guillemaut, Anne; Girodon, Emmanuelle; Remus, Natacha; Bulcaen, Mathis; Ensinck, Marjolein; Zajac, Miroslaw; Carlon, Marianne; LeBihan, Jean; Burgel, Pierre-Régis; Sermet-Gaudelus, Isabelle; Hinzpeter, Alexandre; Pedemonte, Nicoletta

ATP-Binding Cassette and Solute Carrier Transporters: Understanding Their Mechanisms and Drug Modulation Through Structural and Modeling Approaches

ATP结合盒和溶质载体转运蛋白:通过结构和建模方法理解其机制和药物调控

Elbahnsi, Ahmad; Dudas, Balint; Callebaut, Isabelle; Hinzpeter, Alexandre; Miteva, Maria A

Putting bicarbonate on the spot: pharmacological insights for CFTR correction in the airway epithelium

碳酸氢盐直达病灶:气道上皮中CFTR校正的药理学见解

Zajac, Miroslaw; Lepissier, Agathe; Dréano, Elise; Chevalier, Benoit; Hatton, Aurélie; Kelly-Aubert, Mairead; Guidone, Daniela; Planelles, Gabrielle; Edelman, Aleksander; Girodon, Emmanuelle; Hinzpeter, Alexandre; Crambert, Gilles; Pranke, Iwona; Galietta, Luis J V; Sermet-Gaudelus, Isabelle

Elexacaftor/Tezacaftor/Ivacaftor Disrupts Respiratory Tract Development in a Murine Fetal Lung Explant Model

Elexacaftor/Tezacaftor/Ivacaftor 会干扰小鼠胎肺外植体模型中的呼吸道发育

Lhuillier, Mickaël; Aoust, Laura; Dreano, Elise; Franco-Montoya, Marie-Laure; Landry-Truchon, Kim; Houde, Nicolas; Chhun, Stéphanie; Hinzpeter, Alexandre; Edelman, Aleksander; Delacourt, Christophe; Jeannotte, Lucie; Sermet-Gaudelus, Isabelle; Hadchouel, Alice

Systemic bis-phosphinic acid derivative restores chloride transport in Cystic Fibrosis mice

全身性双膦酸衍生物可恢复囊性纤维化小鼠的氯离子转运

da Cunha, Mélanie Faria; Pranke, Iwona; Sassi, Ali; Schreiweis, Christiane; Moriceau, Stéphanie; Vidovic, Dragana; Hatton, Aurélie; Carlon, Mariane Sylvia; Creste, Geordie; Berhal, Farouk; Prestat, Guillaume; Freund, Romain; Odolczyk, Norbert; Jais, Jean Philippe; Gravier-Pelletier, Christine; Zielenkiewicz, Piotr; Jullien, Vincent; Hinzpeter, Alexandre; Oury, Franck; Edelman, Aleksander; Sermet-Gaudelus, Isabelle

Pharmacological chaperones improve intra-domain stability and inter-domain assembly via distinct binding sites to rescue misfolded CFTR

药理学伴侣蛋白通过不同的结合位点改善结构域内稳定性并促进结构域间组装,从而挽救错误折叠的CFTR蛋白。

Baatallah, Nesrine; Elbahnsi, Ahmad; Mornon, Jean-Paul; Chevalier, Benoit; Pranke, Iwona; Servel, Nathalie; Zelli, Renaud; Décout, Jean-Luc; Edelman, Aleksander; Sermet-Gaudelus, Isabelle; Callebaut, Isabelle; Hinzpeter, Alexandre

Author Correction: New insights into structure and function of bis-phosphinic acid derivatives and implications for CFTR modulation

作者更正:双膦酸衍生物的结构和功能的新见解及其对CFTR调控的影响

Bitam, Sara; Elbahnsi, Ahmad; Creste, Geordie; Pranke, Iwona; Chevalier, Benoit; Berhal, Farouk; Hoffmann, Brice; Servel, Nathalie; Baatalah, Nesrine; Tondelier, Danielle; Hatton, Aurelie; Moquereau, Christelle; Faria Da Cunha, Mélanie; Pastor, Alexandra; Lepissier, Agathe; Hinzpeter, Alexandre; Mornon, Jean-Paul; Prestat, Guillaume; Edelman, Aleksander; Callebaut, Isabelle; Gravier-Pelletier, Christine; Sermet-Gaudelus, Isabelle

Alternative splicing at a NAGNAG acceptor site as a novel phenotype modifier.

NAGNAG 受体位点的选择性剪接作为新型表型修饰剂

Hinzpeter Alexandre, Aissat Abdel, Sondo Elvira, Costa Catherine, Arous Nicole, Gameiro Christine, Martin Natacha, Tarze Agathe, Weiss Laurence, de Becdelièvre Alix, Costes Bruno, Goossens Michel, Galietta Luis J, Girodon Emmanuelle, Fanen Pascale

Mutation-specific potency and efficacy of cystic fibrosis transmembrane conductance regulator chloride channel potentiators

囊性纤维化跨膜电导调节因子氯离子通道增强剂的突变特异性效力和功效

Caputo, Antonella; Hinzpeter, Alexandre; Caci, Emanuela; Pedemonte, Nicoletta; Arous, Nicole; Di Duca, Marco; Zegarra-Moran, Olga; Fanen, Pascale; Galietta, Luis J V

The functioning of mammalian ClC-2 chloride channel in Saccharomyces cerevisiae cells requires an increased level of Kha1p

酿酒酵母细胞中哺乳动物ClC-2氯离子通道的功能需要Kha1p水平升高。

Flis, Krzysztof; Hinzpeter, Alexandre; Edelman, Aleksander; Kurlandzka, Anna