日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Restoring early postnatal synaptic dysregulation rescues motor neuron degeneration in a mouse model of Spinal and Bulbar Muscular Atrophy.

恢复早期出生后突触功能障碍可以挽救脊髓延髓肌萎缩症小鼠模型中的运动神经元退化。

Hirunagi Tomoki, Sahashi Kentaro, Iida Madoka, Onodera Kazunari, Yokoi Satoshi, Ogura Yosuke, Tohnai Genki, Sakakibara Kenji, Maeda Kentaro, Bennett C Frank, Okada Yohei, Katsuno Masahisa

An acyclic nucleic acid-modified siRNA targeting CAG expansions for polyglutamine disease treatment.

一种靶向 CAG 扩增的非环状核酸修饰 siRNA,用于治疗多聚谷氨酰胺疾病。

Maeda Kentaro, Hirunagi Tomoki, Sahashi Kentaro, Kamiya Yukiko, Iida Madoka, Sakakibara Kenji, Onodera Kazunari, Ohyama Manabu, Okada Yohei, Okano Hideyuki, Asanuma Hiroyuki, Katsuno Masahisa

Label-free morphology-based phenotypic analysis of spinal and bulbar muscular atrophy muscle cell models.

基于无标记形态学的脊髓延髓肌萎缩症肌细胞模型表型分析

Sakakibara Kenji, Tanaka Kenjiro, Iida Madoka, Imai Yuta, Okada Mai, Sahashi Kentaro, Hirunagi Tomoki, Maeda Kentaro, Kato Ryuji, Katsuno Masahisa

Acute bilateral hypotropia and esotropia complex as first manifestation of multiple sclerosis: a case report

急性双侧下斜视和内斜视复合征作为多发性硬化症的首发表现:病例报告

Senda, Joe; Hirao, Ryota; Maeda, Kentaro; Amakusa, Yoshinobu; Hirunagi, Tomoki; Katsuno, Masahisa; Kawaguchi, Katsuhiro

Nucleic Acid-Based Therapeutic Approach for Spinal and Bulbar Muscular Atrophy and Related Neurological Disorders

基于核酸的脊髓延髓肌萎缩症及相关神经系统疾病治疗方法

Hirunagi, Tomoki; Sahashi, Kentaro; Meilleur, Katherine G; Katsuno, Masahisa