日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Comparative study on incorporation of three recombinant human α-galactosidase A drugs (agalsidases) into cultured fibroblasts and organs/tissues of Fabry mice

三种重组人 α-半乳糖苷酶 A 药物(阿加糖苷酶)与法布里病小鼠培养成纤维细胞和器官/组织结合的比较研究

Takahiro Tsukimura, Tomoko Shiga, Tadayasu Togawa, Hitoshi Sakuraba

Does administration of hydroxychloroquine/amiodarone affect the efficacy of enzyme replacement therapy for Fabry mice?

羟氯喹/胺碘酮的使用是否会影响法布里小鼠酶替代疗法的疗效?

Takahiro Tsukimura, Koki Saito, Tomoko Shiga, Yasuhiro Ogawa, Hitoshi Sakuraba, Tadayasu Togawa

In Vivo Delivery of Therapeutic Molecules by Transplantation of Genome-Edited Induced Pluripotent Stem Cells

通过移植基因组编辑的诱导性多能干细胞进行体内治疗分子递送

Ittetsu Nakajima, Takahiro Tsukimura, Terumi Ono, Tomoko Shiga, Hiroshi Shitara, Tadayasu Togawa, Hitoshi Sakuraba, Yuichiro Miyaoka

Genetically Modified Cell Transplantation Through Macroencapsulated Spheroids with Scaffolds to Treat Fabry Disease

通过带有支架的大胶囊球体进行转基因细胞移植治疗法布里病

Daisuke Kami, Yosuke Suzuki, Masashi Yamanami, Takahiro Tsukimura, Tadayasu Togawa, Hitoshi Sakuraba, Satoshi Gojo

Does administration of hydroxychloroquine/amiodarone accelerate accumulation of globotriaosylceramide and globotriaosylsphingosine in Fabry mice?

服用羟氯喹/胺碘酮是否会加速法布里病小鼠体内神经酰胺三己糖和神经酰胺三己糖的积累?

Takahiro Tsukimura, Tomoko Shiga, Koki Saito, Yasuhiro Ogawa, Hitoshi Sakuraba, Tadayasu Togawa

Cell Transplantation Combined with Recombinant Collagen Peptides for the Treatment of Fabry Disease

细胞移植联合重组胶原蛋白肽治疗法布里病

Daisuke Kami, Masashi Yamanami, Takahiro Tsukimura, Hideki Maeda, Tadayasu Togawa, Hitoshi Sakuraba, Satoshi Gojo

Abnormal organization during neurodevelopment in a mouse model of Sandhoff disease

桑德霍夫病小鼠模型中神经发育过程中的异常组织

Yasuhiro Ogawa, Yayoi Sasanuma, Shuhei Shitara, Asuna Koshizuka, Rieko Okada, Hitoshi Sakuraba, Kazuhiko Oishi

Surface plasmon resonance analysis of complex formation of therapeutic recombinant lysosomal enzymes with domain 9 of human cation-independent mannose 6-phosphate receptor

治疗性重组溶酶体酶与人类阳离子非依赖性甘露糖-6-磷酸受体结构域 9 的复合物形成的表面等离子体共振分析

Minori Kanzaki, Takahiro Tsukimura, Yasunori Chiba, Hitoshi Sakuraba, Tadayasu Togawa

Anti-drug antibody formation in Japanese Fabry patients following enzyme replacement therapy

日本法布里病患者接受酶替代疗法后形成抗药抗体

Takahiro Tsukimura, Yuya Tayama, Tomoko Shiga, Kanako Hirai, Tadayasu Togawa, Hitoshi Sakuraba

Fabry disease in a Japanese population-molecular and biochemical characteristics

日本人群中的法布里病——分子和生化特征

Hitoshi Sakuraba, Takahiro Tsukimura, Tadayasu Togawa, Toshie Tanaka, Tomoko Ohtsuka, Atsuko Sato, Tomoko Shiga, Seiji Saito, Kazuki Ohno