Evaluating the feasibility of gene replacement strategies to treat MTRFR deficiency.
评估基因替代策略治疗 MTRFR 缺乏症的可行性
期刊:Disease Models & Mechanisms
影响因子:3.3
doi:10.1242/dmm.052120
Pratt Samia L, Zarate-Mendez Mariana, Koludarova Lidiia, Jansson Sonja, Airavaara Mikko, Hlushchuk Irena, Coleman David, Heffner Caleb, Horvath Rita, Battersby Brendan J, Burgess Robert W