日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A region-delineated snRNA-seq atlas of mouse spinal cord across lifespan resolves the interaction of normative aging programs with SOD1-G93A ALS

小鼠脊髓终生区域性snRNA测序图谱揭示了正常衰老程序与SOD1-G93A ALS的相互作用

Ramos, Michael Edison Pauli; Singh, Brijesh Kumar; Shelest, Oksana; Tindel, Ian; Zogu, Benisa; Dawson, Ashley; Mathkar, Pranav; Bell, Shaughn; Ho, Ritchie

Targeted Proteomics upon Treatment with Tofersen Identifies Novel Response Markers for Superoxide Dismutase 1-Linked Amyotrophic Lateral Sclerosis

托弗森治疗后的靶向蛋白质组学鉴定出超氧化物歧化酶 1 相关肌萎缩侧索硬化症的新型反应标志物

Steffke, Christina; Baskar, Karthik; Bachhuber, Franziska; Wiesenfarth, Maximilian; Dorst, Johannes; Schuster, Joachim; Schöberl, Florian; Reilich, Peter; Regensburger, Martin; German, Alexander; Günther, René; Vidovic, Maximilian; Petri, Susanne; Meyer, Thomas; Hagenacker, Tim; Grosskreutz, Julian; Weyen, Ute; Weydt, Patrick; Haarmeier, Thomas; Lingor, Paul; Wolf, Joachim; Hermann, Andreas; Prudlo, Johannes; Günther, Kornelia; Knehr, Antje; Elmas, Zeynep; Uzelac, Zeljko; Witzel, Simon; Ruf, Wolfgang Philipp; Freischmidt, Axel; Ho, Ritchie; Ludolph, Albert C; Weishaupt, Jochen H; Tumani, Hayrettin; Oeckl, Patrick; Brenner, David; Catanese, Alberto

The myokine FGF21 associates with enhanced survival in ALS and mitigates stress-induced cytotoxicity

肌细胞因子FGF21与ALS患者的生存率提高有关,并能减轻应激诱导的细胞毒性。

Guha, Abhishek; Si, Ying; Smith, Reed; Singh, Brijesh K; Zogu, Benisa; Yadav, Angad; Smith, Katherine A; Kazamel, Mohamed; Jiang, Nan; Ho, Ritchie; Thalacker-Mercer, Anna; Andrabi, Shaida A; Da Silva Pereira, Joao D Tavares; Salgado, Juliana S; Agrawal, Manasi; Velic, Emina Horvat; King, Peter H

Multi-lineage heart-chip models drug cardiotoxicity and enhances maturation of human stem cell-derived cardiovascular cells.

多谱系心脏芯片模拟药物心脏毒性,并促进人类干细胞衍生心血管细胞的成熟

Mozneb Maedeh, Jenkins Amelia, Sances Samuel, Pohlman Stephany, Workman Michael J, West Dylan, Ondatje Briana, El-Ghazawi Kareem, Woodbury Amanda, Garcia Veronica J, Patel Shachi, Arzt Madelyn, Dezem Felipe, Laperle Alex H, Moser V Alexandra, Ho Ritchie, Yucer Nur, Plummer Jasmine, Barrett Robert J, Svendsen Clive N, Sharma Arun

CRISPR/Cas9 screen in human iPSC-derived cortical neurons identifies NEK6 as a novel disease modifier of C9orf72 poly(PR) toxicity

利用 CRISPR/Cas9 技术在人类 iPSC 衍生的皮层神经元中进行筛选,发现 NEK6 是 C9orf72 poly(PR) 毒性的新型疾病修饰因子。

Guo, Wenting; Wang, Haibo; Kumar Tharkeshwar, Arun; Couthouis, Julien; Braems, Elke; Masrori, Pegah; Van Schoor, Evelien; Fan, Yannan; Ahuja, Karan; Moisse, Matthieu; Jacquemyn, Maarten; Furtado Madeiro da Costa, Rodrigo; Gajjar, Madhavsai; Balusu, Sriram; Tricot, Tine; Fumagalli, Laura; Hersmus, Nicole; Janky, Rekin's; Impens, Francis; Vanden Berghe, Pieter; Ho, Ritchie; Thal, Dietmar Rudolf; Vandenberghe, Rik; Hegde, Muralidhar L; Chandran, Siddharthan; De Strooper, Bart; Daelemans, Dirk; Van Damme, Philip; Van Den Bosch, Ludo; Verfaillie, Catherine

Human iPSC-derived neural progenitor cells secreting GDNF provide protection in rodent models of ALS and retinal degeneration

分泌GDNF的人类iPSC衍生神经祖细胞在ALS和视网膜变性啮齿动物模型中提供保护作用。

Laperle, Alexander H; Moser, V Alexandra; Avalos, Pablo; Lu, Bin; Wu, Amanda; Fulton, Aaron; Ramirez, Stephany; Garcia, Veronica J; Bell, Shaughn; Ho, Ritchie; Lawless, George; Roxas, Kristina; Shahin, Saba; Shelest, Oksana; Svendsen, Soshana; Wang, Shaomei; Svendsen, Clive N

Restoring mitofusin balance prevents axonal degeneration in a Charcot-Marie-Tooth type 2A model

恢复线粒体融合蛋白平衡可预防夏科-马里-图斯病 2A 型模型中的轴突变性

Zhou, Yueqin; Carmona, Sharon; Muhammad, A K M G; Bell, Shaughn; Landeros, Jesse; Vazquez, Michael; Ho, Ritchie; Franco, Antonietta; Lu, Bin; Dorn, Gerald W 2nd; Wang, Shaomei; Lutz, Cathleen M; Baloh, Robert H

The Library of Integrated Network-Based Cellular Signatures NIH Program: System-Level Cataloging of Human Cells Response to Perturbations

美国国立卫生研究院(NIH)项目“基于网络的细胞特征库”:人类细胞对扰动反应的系统级编目

Keenan, Alexandra B; Jenkins, Sherry L; Jagodnik, Kathleen M; Koplev, Simon; He, Edward; Torre, Denis; Wang, Zichen; Dohlman, Anders B; Silverstein, Moshe C; Lachmann, Alexander; Kuleshov, Maxim V; Ma'ayan, Avi; Stathias, Vasileios; Terryn, Raymond; Cooper, Daniel; Forlin, Michele; Koleti, Amar; Vidovic, Dusica; Chung, Caty; Schürer, Stephan C; Vasiliauskas, Jouzas; Pilarczyk, Marcin; Shamsaei, Behrouz; Fazel, Mehdi; Ren, Yan; Niu, Wen; Clark, Nicholas A; White, Shana; Mahi, Naim; Zhang, Lixia; Kouril, Michal; Reichard, John F; Sivaganesan, Siva; Medvedovic, Mario; Meller, Jaroslaw; Koch, Rick J; Birtwistle, Marc R; Iyengar, Ravi; Sobie, Eric A; Azeloglu, Evren U; Kaye, Julia; Osterloh, Jeannette; Haston, Kelly; Kalra, Jaslin; Finkbiener, Steve; Li, Jonathan; Milani, Pamela; Adam, Miriam; Escalante-Chong, Renan; Sachs, Karen; Lenail, Alex; Ramamoorthy, Divya; Fraenkel, Ernest; Daigle, Gavin; Hussain, Uzma; Coye, Alyssa; Rothstein, Jeffrey; Sareen, Dhruv; Ornelas, Loren; Banuelos, Maria; Mandefro, Berhan; Ho, Ritchie; Svendsen, Clive N; Lim, Ryan G; Stocksdale, Jennifer; Casale, Malcolm S; Thompson, Terri G; Wu, Jie; Thompson, Leslie M; Dardov, Victoria; Venkatraman, Vidya; Matlock, Andrea; Van Eyk, Jennifer E; Jaffe, Jacob D; Papanastasiou, Malvina; Subramanian, Aravind; Golub, Todd R; Erickson, Sean D; Fallahi-Sichani, Mohammad; Hafner, Marc; Gray, Nathanael S; Lin, Jia-Ren; Mills, Caitlin E; Muhlich, Jeremy L; Niepel, Mario; Shamu, Caroline E; Williams, Elizabeth H; Wrobel, David; Sorger, Peter K; Heiser, Laura M; Gray, Joe W; Korkola, James E; Mills, Gordon B; LaBarge, Mark; Feiler, Heidi S; Dane, Mark A; Bucher, Elmar; Nederlof, Michel; Sudar, Damir; Gross, Sean; Kilburn, David F; Smith, Rebecca; Devlin, Kaylyn; Margolis, Ron; Derr, Leslie; Lee, Albert; Pillai, Ajay

Human iPSC-Derived Endothelial Cells and Microengineered Organ-Chip Enhance Neuronal Development

人诱导多能干细胞衍生的内皮细胞和微工程器官芯片可促进神经元发育

Sances, Samuel; Ho, Ritchie; Vatine, Gad; West, Dylan; Laperle, Alex; Meyer, Amanda; Godoy, Marlesa; Kay, Paul S; Mandefro, Berhan; Hatata, Seigo; Hinojosa, Chris; Wen, Norman; Sareen, Dhruv; Hamilton, Geraldine A; Svendsen, Clive N

Modeling ALS with motor neurons derived from human induced pluripotent stem cells

利用源自人类诱导多能干细胞的运动神经元构建ALS模型

Sances, Samuel; Bruijn, Lucie I; Chandran, Siddharthan; Eggan, Kevin; Ho, Ritchie; Klim, Joseph R; Livesey, Matt R; Lowry, Emily; Macklis, Jeffrey D; Rushton, David; Sadegh, Cameron; Sareen, Dhruv; Wichterle, Hynek; Zhang, Su-Chun; Svendsen, Clive N