日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Discovery of Zilucoplan: A Complement C5 Inhibitor for Treatment of Anti-Acetylcholine Receptor (AChR) Antibody-Positive Generalized Myasthenia Gravis (gMG)

Zilucoplan 的发现:一种用于治疗抗乙酰胆碱受体 (AChR) 抗体阳性全身型重症肌无力 (gMG) 的补体 C5 抑制剂

Ye, Ping; Hammer, Robert P; Wang, Zhaolin; Dhamnaskar, Ketki; Hoarty, Michelle; Ma, Zhong; Tang, Guo-Qing; DeMarco, Steven J; Ricardo, Alonso

Zilucoplan, a macrocyclic peptide inhibitor of human complement component 5, uses a dual mode of action to prevent terminal complement pathway activation

Zilucoplan 是一种人类补体成分 5 的大环肽抑制剂,采用双重作用模式来阻止终末补体途径激活

Guo-Qing Tang, Yalan Tang, Ketki Dhamnaskar, Michelle D Hoarty, Rohit Vyasamneni, Douangsone D Vadysirisack, Zhong Ma, Nanqun Zhu, Jian-Guo Wang, Charlie Bu, Bestine Cong, Elizabeth Palmer, Petra W Duda, Camil Sayegh, Alonso Ricardo

Clinical Effects of the Self-administered Subcutaneous Complement Inhibitor Zilucoplan in Patients With Moderate to Severe Generalized Myasthenia Gravis: Results of a Phase 2 Randomized, Double-Blind, Placebo-Controlled, Multicenter Clinical Trial

自我注射皮下补体抑制剂齐鲁普兰治疗中重度全身型重症肌无力患者的临床疗效:一项 II 期随机、双盲、安慰剂对照、多中心临床试验的结果

Howard, James F Jr; Nowak, Richard J; Wolfe, Gil I; Freimer, Miriam L; Vu, Tuan H; Hinton, John L; Benatar, Michael; Duda, Petra W; MacDougall, James E; Farzaneh-Far, Ramin; Kaminski, Henry J; Barohn, Richard; Dimachkie, Mazen; Pasnoor, Mamatha; Farmakidis, Constantine; Liu, Tina; Colgan, Samantha; Benatar, Michael G; Bertorini, Tulio; Pillai, Rekha; Henegar, Robert; Bromberg, Mark; Gibson, Summer; Janecki, Teresa; Freimer, Miriam; Elsheikh, Bakri; Matisak, Paige; Genge, Angela; Guidon, Amanda; David, William; Habib, Ali A; Mathew, Veena; Mozaffar, Tahseen; Hinton, John L; Hewitt, William; Barnett, Deborah; Sullivan, Patricia; Ho, Doreen; Howard, James F Jr; Traub, Rebecca E; Chopra, Manisha; Kaminski, Henry J; Aly, Radwa; Bayat, Elham; Abu-Rub, Mohammad; Khan, Shaida; Lange, Dale; Holzberg, Shara; Khatri, Bhupendra; Lindman, Emily; Olapo, Tayo; Sershon, Lisa M; Lisak, Robert P; Bernitsas, Evanthia; Jia, Kelly; Malik, Rabia; Lewis-Collins, Tiffany D; Nicolle, Michael; Nowak, Richard J; Sharma, Aditi; Roy, Bhaskar; Nye, Joan; Pulley, Michael; Berger, Alan; Shabbir, Yasmeen; Sachdev, Amit; Patterson, Kimberly; Siddiqi, Zaeem; Sivak, Mark; Bratton, Joan; Small, George; Kohli, Anem; Fetter, Mary; Vu, Tuan; Lam, Lucy; Harvey, Brittany; Wolfe, Gil I; Silvestri, Nicholas; Patrick, Kara; Zakalik, Karen; Duda, Petra W; MacDougall, James; Farzaneh-Far, Ramin; Pontius, Angela; Hoarty, Michelle

Treadmill gait speeds correlate with physical activity counts measured by cell phone accelerometers

跑步机步速与手机加速度计测量的身体活动量呈正相关

Carlson, Richard H Jr; Huebner, Derek R; Hoarty, Carrie A; Whittington, Jackie; Haynatzki, Gleb; Balas, Michele C; Schenk, Ana Katrin; Goulding, Evan H; Potter, Jane F; Bonasera, Stephen J

Cellular telephones measure activity and lifespace in community-dwelling adults: proof of principle

利用手机测量社区居住成年人的活动和生活空间:原理验证

Schenk, Ana Katrin; Witbrodt, Bradley C; Hoarty, Carrie A; Carlson, Richard H Jr; Goulding, Evan H; Potter, Jane F; Bonasera, Stephen J