Sustained high expression of human FVII following AAV8-mediated gene delivery in mice.
在小鼠体内通过 AAV8 介导的基因递送实现人 FVII 的持续高表达
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2025.101523
D'Amico Andrea, Blits Bas, van den Herik Joëlle, de Winter Fred, Kaijen Paul H P, Hobo Barbara, van Asbeck Alexander Henrik, Verhaagen Joost, Mosmuller David G M, Voorberg Jan