日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Could an outcome-based agreement be operationalized using real-world data from the Canadian Neuromuscular Disease Registry? Perspectives from an expert-led assessment in spinal muscular atrophy

能否利用加拿大神经肌肉疾病登记处的真实世界数据来实施基于结果的协议?来自脊髓性肌萎缩症专家主导评估的视角

Mitha, Arif; Hodgkinson, Victoria; Vander Wyk, Susi; Cameron, Chris; Wills, Allison

Actions for stakeholders to develop better real-world evidence for HTA bodies/payers decision making

利益相关者应采取行动,为卫生技术评估机构/支付方决策提供更好的真实世界证据。

Jaksa, Ashley A; Pavel, Alina N; Aapro, Matti; Hedberg, Niklas; Hodgkinson, Victoria; Lambert, Laurie J; Meyer, Francois; Olsen, Matias; Rannanheimo, Piia K; Facey, Karen M

Facial/sinus pain or pressure and migraine: exploratory findings from the HEADS registry

面部/鼻窦疼痛或压迫感与偏头痛:来自 HEADS 注册研究的探索性发现

Kuruvilla, Deena E; Tietjen, Gretchen E; Panza, Gregory A; Hodgkinson, Victoria L; Godley, Frederick A 3rd

A Canadian Adult Spinal Muscular Atrophy Outcome Measures Toolkit: Results of a National Consensus using a Modified Delphi Method

加拿大成人脊髓性肌萎缩症结局指标工具包:采用改良德尔菲法的全国共识结果

Slayter, Jeremy; Hodgkinson, Victoria; Lounsberry, Josh; Brais, Bernard; Chapman, Kristine; Genge, Angela; Izenberg, Aaron; Johnston, Wendy; Lochmüller, Hanns; O'Ferrall, Erin; Pfeffer, Gerald; Plamondon, Stephanie; Rodrigue, Xavier; Schellenberg, Kerri; Shoesmith, Christen; Stables, Christine; Taillon, Monique; Warman-Chardon, Jodi; Korngut, Lawrence; O'Connell, Colleen

A National Spinal Muscular Atrophy Registry for Real-World Evidence

国家脊髓性肌萎缩症真实世界证据登记处

Hodgkinson, Victoria L; Oskoui, Maryam; Lounsberry, Joshua; M'Dahoma, Saïd; Butler, Emily; Campbell, Craig; MacKenzie, Alex; McMillan, Hugh J; Simard, Louise; Vajsar, Jiri; Brais, Bernard; Chapman, Kristine M; Chrestian, Nicolas; Crone, Meghan; Dobrowolski, Peter; Dojeiji, Susan; Dowling, James J; Dupré, Nicolas; Genge, Angela; Gonorazky, Hernan; Hasal, Simona; Izenberg, Aaron; Johnston, Wendy; Leung, Edward; Lochmüller, Hanns; Mah, Jean K; Marerro, Alier; Massie, Rami; McAdam, Laura; McCormick, Anna; Melanson, Michel; Mezei, Michelle M; Nguyen, Cam-Tu E; O'Connell, Colleen; O'Ferrall, Erin K; Pfeffer, Gerald; Phan, Cecile; Plamondon, Stephanie; Poulin, Chantal; Rodrigue, Xavier; Schellenberg, Kerri L; Selby, Kathy; Sheriko, Jordan; Shoesmith, Christen; Smith, Garth; Taillon, Monique; Taylor, Sean; Warman Chardon, Jodi; Worley, Scott; Korngut, Lawrence

Clinically Meaningful Difference for the Infant Gastroesophageal Questionnaire Revised version (I-GERQ-R): A Quantitative Synthesis

婴儿胃食管问卷修订版(I-GERQ-R)的临床意义差异:一项定量综合研究

Smith, Adam B; Fawkes, Neil; Kotze, Helen; Hodgkinson, Victoria; Coyle, Cathal

The Canadian Neuromuscular Disease Registry: Connecting patients to national and international research opportunities

加拿大神经肌肉疾病登记处:连接患者与国内和国际研究机会

Wei, Yi; McCormick, Anna; MacKenzie, Alex; O'Ferrall, Erin; Venance, Shannon; Mah, Jean K; Selby, Kathryn; McMillan, Hugh J; Smith, Garth; Oskoui, Maryam; Hogan, Gillian; McAdam, Laura; Mabaya, Gracia; Hodgkinson, Victoria; Lounsberry, Josh; Korngut, Lawrence; Campbell, Craig

Multiple di-leucines in the ATP7A copper transporter are required for retrograde trafficking to the trans-Golgi network

ATP7A铜转运蛋白中的多个二亮氨酸残基是逆向运输至反式高尔基网络所必需的。

Zhu, Sha; Shanbhag, Vinit; Hodgkinson, Victoria L; Petris, Michael J

X-linked spinal muscular atrophy in mice caused by autonomous loss of ATP7A in the motor neuron

小鼠X连锁脊髓性肌萎缩症是由运动神经元中ATP7A的自主性缺失引起的

Hodgkinson, Victoria L; Dale, Jeffery M; Garcia, Michael L; Weisman, Gary A; Lee, Jaekwon; Gitlin, Jonathan D; Petris, Michael J

Autonomous requirements of the Menkes disease protein in the nervous system

Menkes病蛋白在神经系统中的自主需求

Hodgkinson, Victoria L; Zhu, Sha; Wang, Yanfang; Ladomersky, Erik; Nickelson, Karen; Weisman, Gary A; Lee, Jaekwon; Gitlin, Jonathan D; Petris, Michael J