A National Spinal Muscular Atrophy Registry for Real-World Evidence
国家脊髓性肌萎缩症真实世界证据登记处
期刊:Canadian Journal of Neurological Sciences
影响因子:2.2
doi:10.1017/cjn.2020.111
Hodgkinson, Victoria L; Oskoui, Maryam; Lounsberry, Joshua; M'Dahoma, Saïd; Butler, Emily; Campbell, Craig; MacKenzie, Alex; McMillan, Hugh J; Simard, Louise; Vajsar, Jiri; Brais, Bernard; Chapman, Kristine M; Chrestian, Nicolas; Crone, Meghan; Dobrowolski, Peter; Dojeiji, Susan; Dowling, James J; Dupré, Nicolas; Genge, Angela; Gonorazky, Hernan; Hasal, Simona; Izenberg, Aaron; Johnston, Wendy; Leung, Edward; Lochmüller, Hanns; Mah, Jean K; Marerro, Alier; Massie, Rami; McAdam, Laura; McCormick, Anna; Melanson, Michel; Mezei, Michelle M; Nguyen, Cam-Tu E; O'Connell, Colleen; O'Ferrall, Erin K; Pfeffer, Gerald; Phan, Cecile; Plamondon, Stephanie; Poulin, Chantal; Rodrigue, Xavier; Schellenberg, Kerri L; Selby, Kathy; Sheriko, Jordan; Shoesmith, Christen; Smith, Garth; Taillon, Monique; Taylor, Sean; Warman Chardon, Jodi; Worley, Scott; Korngut, Lawrence