日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Once-Weekly Navepegritide in Children With Achondroplasia: The APPROACH Randomized Clinical Trial

每周一次使用萘培格里肽治疗软骨发育不全患儿:APPROACH随机临床试验

Savarirayan, Ravi; McDonnell, Ciara; Bacino, Carlos A; Hoernschemeyer, Daniel G; Legare, Janet M; Abuzzahab, M Jennifer; Hofman, Paul L; Campeau, Philippe M; de Bergua Domingo, Josep Maria; Ward, Leanne M; Smit, Kevin; Smith, Alden; Mao, Meng; Ominsky, Michael S; Freiberg, Lærke C; Shu, Aimee D; Hove, Hanne B

Longitudinal Observation of Children with Achondroplasia: Findings from a Global Natural History Study (ACHieve)

对软骨发育不全患儿的纵向观察:一项全球自然史研究(ACHieve)的发现

McDonnell, Ciara; Hove, Hanne Buciek; Irving, Melita; White, Klane K; Fontecha, Cesar G; Legare, Janet M; Högler, Wolfgang; Hoernschemeyer, Daniel G; Schnabel, Dirk; Unger, Sheila; Bacino, Carlos Alberto; Hofman, Paul; Yu, Yongguo; Ma, Huamei; Gong, Chunxiu; Luo, Xiaoping; Burrow, T Andrew; Baujat, Geneviève; Mora, Stefano; Fiscaletti, Melissa; Zhao, Carol; Makara, Michael A; Shu, Aimee D; Savarirayan, Ravi

Lived Experiences of Vertebral Body Tethering: A Qualitative Study of the Patient Journey

椎体束缚术患者的真实体验:一项关于患者历程的定性研究

Royse, Lisa A; Saparova, Dinara; Boeyer, Melanie E; Hoernschemeyer, Daniel G

Once-weekly TransCon CNP (navepegritide) in children with achondroplasia (ACcomplisH): a phase 2, multicentre, randomised, double-blind, placebo-controlled, dose-escalation trial

每周一次TransCon CNP(navepegritide)治疗软骨发育不全患儿(ACcomplisH):一项II期、多中心、随机、双盲、安慰剂对照、剂量递增试验

Savarirayan, Ravi; Hoernschemeyer, Daniel G; Ljungberg, Merete; Zarate, Yuri A; Bacino, Carlos A; Bober, Michael B; Legare, Janet M; Högler, Wolfgang; Quattrin, Teresa; Abuzzahab, M Jennifer; Hofman, Paul L; White, Klane K; Ma, Nina S; Schnabel, Dirk; Sousa, Sérgio B; Mao, Meng; Smith, Alden; Chakraborty, Mukta; Giwa, Adebola; Winding, Bent; Volck, Birgitte; Shu, Aimee D; McDonnell, Ciara

Persistent and Stable Growth Promoting Effects of Vosoritide in Children With Achondroplasia for up to 2 Years: Results From the Ongoing Phase 3 Extension Study

Vosoritide 对软骨发育不全患儿的生长促进作用可持续长达 2 年:正在进行的 3 期扩展研究的结果

Zhang, Dazheng; Tong, Jiayi; Stein, Ronen; Lu, Yiwen; Jing, Naimin; Yang, Yuchen; Boland, Mary R; Luo, Chongliang; Baldassano, Robert N; Carroll, Raymond J; Forrest, Christopher B; Chen, Yong; Savarirayan, Ravi; Tofts, Louise; Irving, Melita; Wilcox, William; Bacino, Carlos A; Hoover-Fong, Julie; Font, Rosendo Ullot; Harmatz, Paul; Rutsch, Frank; Bober, Michael B; Polgreen, Lynda; Ginebreda, Ignacio; Mohnike, Klaus; Charrow, Joel; Hoernschemeyer, Daniel; Ozono, Keiichi; Alanay, Yasemin; Arundel, Paul; Kagami, Shoji; Yasui, Natsuo; White, Klane; Saal, Howard; Leiva-Gea, Antonio; Luna-González, Felipe; Mochizuki, Hiroshi; Basel, Donald; Porco, Dania; Jayaram, Kala; Fisheleva, Elena; Han, Lynn; Day, Jonathan

Potent and Selective BACE-1 Peptide Inhibitors Lower Brain Aβ Levels Mediated by Brain Shuttle Transport

强效且选择性的 BACE-1 肽抑制剂通过脑穿梭运输降低脑 Aβ 水平

Nadine Ruderisch, Daniel Schlatter, Andreas Kuglstatter, Wolfgang Guba, Sylwia Huber, Carlo Cusulin, Jörg Benz, Arne Christian Rufer, Joerg Hoernschemeyer, Christophe Schweitzer, Tina Bülau, Achim Gärtner, Eike Hoffmann, Jens Niewoehner, Christoph Patsch, Karlheinz Baumann, Hansruedi Loetscher, Eric

Structure of the malaria vaccine candidate antigen CyRPA and its complex with a parasite invasion inhibitory antibody

疟疾疫苗候选抗原 CyRPA 及其与寄生虫侵袭抑制抗体的复合物的结构

Paola Favuzza, Elena Guffart, Marco Tamborrini, Bianca Scherer, Anita M Dreyer, Arne C Rufer, Johannes Erny, Joerg Hoernschemeyer, Ralf Thoma, Georg Schmid, Bernard Gsell, Araceli Lamelas, Joerg Benz, Catherine Joseph, Hugues Matile, Gerd Pluschke, Markus G Rudolph