Persistent and Stable Growth Promoting Effects of Vosoritide in Children With Achondroplasia for up to 2 Years: Results From the Ongoing Phase 3 Extension Study
Vosoritide 对软骨发育不全患儿的生长促进作用可持续长达 2 年:正在进行的 3 期扩展研究的结果
期刊:Journal of Biomedical Informatics
影响因子:4.5
doi:10.1016/j.jbi.2024.104595
Zhang, Dazheng; Tong, Jiayi; Stein, Ronen; Lu, Yiwen; Jing, Naimin; Yang, Yuchen; Boland, Mary R; Luo, Chongliang; Baldassano, Robert N; Carroll, Raymond J; Forrest, Christopher B; Chen, Yong; Savarirayan, Ravi; Tofts, Louise; Irving, Melita; Wilcox, William; Bacino, Carlos A; Hoover-Fong, Julie; Font, Rosendo Ullot; Harmatz, Paul; Rutsch, Frank; Bober, Michael B; Polgreen, Lynda; Ginebreda, Ignacio; Mohnike, Klaus; Charrow, Joel; Hoernschemeyer, Daniel; Ozono, Keiichi; Alanay, Yasemin; Arundel, Paul; Kagami, Shoji; Yasui, Natsuo; White, Klane; Saal, Howard; Leiva-Gea, Antonio; Luna-González, Felipe; Mochizuki, Hiroshi; Basel, Donald; Porco, Dania; Jayaram, Kala; Fisheleva, Elena; Han, Lynn; Day, Jonathan