Sonlicromanol improves neuronal network dysfunction and transcriptome changes linked to m.3243A>G heteroplasmy in iPSC-derived neurons
Sonlicromanol 可改善 iPSC 衍生神经元中与 m.3243A>G 异质性相关的神经元网络功能障碍和转录组变化
期刊:Stem Cell Reports
影响因子:5.9
doi:10.1016/j.stemcr.2021.07.002
Teun M Klein Gunnewiek ,Anouk H A Verboven ,Iris Pelgrim ,Mark Hogeweg ,Chantal Schoenmaker ,Herma Renkema ,Julien Beyrath ,Jan Smeitink ,Bert B A de Vries ,Peter-Bram A C 't Hoen ,Tamas Kozicz ,Nael Nadif Kasri