Efficient Cas9 nuclease-based editing in skeletal muscle via lipid nanoparticle delivery
通过脂质纳米颗粒递送在骨骼肌中高效进行基于Cas9核酸酶的基因编辑
期刊:
影响因子:
doi:10.1101/2025.05.12.653518
Iyer, Sukanya; Daman, Katelyn; Sun, Yehui; Tutto, Amanda; Holbrook, Sarah E; Joynt, Anya T; Yan, Jing; Ambegaokar, Prajakta; Guo, Dongsheng; Liu, Pengpeng; Stauffer, Jennifer; Maitland, Stacy A; Lee, Sang M; Gallagher, Thomas L; Cox, Gregory A; Keeler, Allison M; Siegwart, Daniel J; Emerson, Charles P; Wolfe, Scot A