Prime Editor Gene Therapy and TREX1 Mosaicism in Retinal Vasculopathy with Cerebral Leukoencephalopathy.
主编:基因治疗和 TREX1 嵌合体在视网膜血管病变伴脑白质脑病中的作用
期刊:Journal of Clinical Immunology
影响因子:5.7
doi:10.1007/s10875-024-01846-y
Chauvin Samuel D, Holley Joe A, Poddar Subhajit, Miner Cathrine A, Kumble Lindsay, Fu Jiayuan, Laue-Gizzi Hanka, Hardy Todd A, Miner Jonathan J