CRISPR/Cas9-mediated somatic correction of a novel coagulator factor IX gene mutation ameliorates hemophilia in mouse
CRISPR/Cas9 介导的新型凝血因子 IX 基因突变的体细胞校正可改善小鼠的血友病
期刊:EMBO Molecular Medicine
影响因子:9
doi:10.15252/emmm.201506039
Yuting Guan, Yanlin Ma, Qi Li, Zhenliang Sun, Lie Ma, Lijuan Wu, Liren Wang, Li Zeng, Yanjiao Shao, Yuting Chen, Ning Ma, Wenqing Lu, Kewen Hu, Honghui Han, Yanhong Yu, Yuanhua Huang, Mingyao Liu, Dali Li