日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Development of a DUX4-targeting antibody oligonucleotide conjugate as a therapy for FSHD

开发靶向DUX4的抗体寡核苷酸偶联物作为FSHD的治疗方法

Malecova, Barbora; Sala, David; Melikian, Garineh M; Johns, Rachel; Erdogan, Gulin; Hartmann, Marc; Jordan, Maryam; Arias, Joel Danny; Bhattacharya, Arvind; Meng, Qingying; Dansereau, Oliver; Beppler, Samuel W; Doppalapudi, Venkata R; Huang, Hanhua; Flanagan, William Michael; Levin, Arthur A

AOC 1044 induces exon 44 skipping and restores dystrophin protein in preclinical models of Duchenne muscular dystrophy.

AOC 1044 可诱导外显子 44 跳跃,并在杜氏肌营养不良症的临床前模型中恢复肌营养不良蛋白

Etxaniz Usue, Marks Isaac, Albin Tyler, Diaz Matthew, Bhardwaj Raghav, Anderson Aaron, Tyaglo Olecya, Hoang Tiffany, Missinato Maria Azzurra, Svensson Kristoffer, Badillo Ben, Kovach Philip R, Leung Laura, Cochran Michael, Kwon Hae Won, Ahad Shah Md Nur, Maruyama Rika, Yokota Toshifumi, Doppalapudi Venkata R, Darimont Beatrice, Younis Husam S, Flanagan W Michael, Levin Arthur A, Huang Hanhua, Karamanlidis Georgios

Structure-Activity Relationship of Antibody-Oligonucleotide Conjugates: Evaluating Bioconjugation Strategies for Antibody-siRNA Conjugates for Drug Development

抗体-寡核苷酸偶联物的构效关系:评估用于药物开发的抗体-siRNA偶联物的生物偶联策略

Cochran, Michael; Arias, Danny; Burke, Rob; Chu, David; Erdogan, Gulin; Hood, Michael; Kovach, Philip; Kwon, Hae Won; Chen, Yanling; Moon, Michael; Miller, Christopher D; Huang, Hanhua; Levin, Arthur; Doppalapudi, Venkata Ramana

Targeted tissue delivery of RNA therapeutics using antibody-oligonucleotide conjugates (AOCs)

利用抗体-寡核苷酸偶联物(AOCs)进行RNA疗法的靶向组织递送

Malecova, Barbora; Burke, Rob S; Cochran, Michael; Hood, Michael D; Johns, Rachel; Kovach, Philip R; Doppalapudi, Venkata R; Erdogan, Gulin; Arias, J Danny; Darimont, Beatrice; Miller, Christopher D; Huang, Hanhua; Geall, Andrew; Younis, Husam S; Levin, Arthur A