Preclinical Optimization and Safety Studies of a New Lentiviral Gene Therapy for p47(phox)-Deficient Chronic Granulomatous Disease
针对p47(phox)缺陷型慢性肉芽肿病的新型慢病毒基因疗法的临床前优化和安全性研究
期刊:Human Gene Therapy
影响因子:4
doi:10.1089/hum.2020.276
Schejtman, Andrea; Vetharoy, Winston; Choi, Uimook; Rivat, Christine; Theobald, Narda; Piras, Giuseppa; Leon-Rico, Diego; Buckland, Karen; Armenteros-Monterroso, Elena; Benedetti, Sara; Ashworth, Michael T; Rothe, Michael; Schambach, Axel; Gaspar, Hubert Bobby; Kang, Elizabeth M; Malech, Harry L; Thrasher, Adrian J; Santilli, Giorgia
