日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

SpliceHarmonization: an integrated method for identifying RNA splicing events in therapeutics for splicing modulation

SpliceHarmonization:一种用于识别治疗药物中RNA剪接事件以进行剪接调控的综合方法

Chen, Yirui; Zhang, Haotian; Sun, Yu H; Negi, Soumya; Cao, Shaolong; Ouyang, Zhengyu; Zhang, Baohong; Hurt, Jessica; Huh, Dann

Viral-mediated knockdown of Atxn2 attenuates TDP-43 pathology and muscle dysfunction in the PFN1(C71G) ALS mouse model.

病毒介导的 Atxn2 敲低可减轻 PFN1(C71G) ALS 小鼠模型中的 TDP-43 病理和肌肉功能障碍

Hawley Zachary C E, Li Xueying, Bodnar Dora, Gu Yuanzheng, Luo Yi, Ferretti Daniel, Sheehy Adam, Driscoll Rachelle, Zavodszky Maria I, Cao Shaolong, Isaza Isabel, Jandreski Luke, Liu Yuqing, Carlile Thomas, Lo Shih-Ching, Grimard Anna, Bourque Shawn, Utturkar Aditya, Desmarais Samantha, Arnold H Moore, Huh Dann, Guilmette Edward, Kwon Deborah Y

Inhibition of immune response reduces pathology in dorsal root ganglia and peripheral nerves in cynomolgus macaques following AAV gene therapy

抑制免疫反应可减轻食蟹猴在接受腺相关病毒(AAV)基因治疗后背根神经节和周围神经的病理变化。

Grubor, Branka; Henry, Kate L; Chan, Su Jing; Sheehan, Mark; Shah, Anumeha; Pellerin, Alex; Bai, Judy; Nadella, Prasad; Bommegowda, Santhosh; Cullen, Patrick; Tien, Eric; Chen, Vivian; van der Munnik, Nicholas P; White-Hunt, Stephanie; Plowey, Edward D; Hamann, Stefan; Guise, Amanda J; Xu, Shanqin; Kirkland, Melissa; Doherty, Jessica; Lyashenko, Eugenia; Bhat, Guruharsha; Glajch, Kelly; Lo, Shih-Ching; Gianni, Davide; Clarner, Pete; Gagnon, Jake; Chu, Jenhwa; Nambiar, Kalyani; Lulla, Mukesh; Zheng, Fengmei; Weldeab, Asmerom; Bartlett, Dan; Gutnick, Amos; Reynolds, Taylor; Zhu, Kan; Huh, Dann; Carlile, Thomas M; Fikes, James; Trapa, Patrick; Suh, Junghae; Morris, Dale; Burkly, Linda

Author Correction: Transcriptional characterization of iPSC-derived microglia as a model for therapeutic development in neurodegeneration

作者更正:iPSC衍生小胶质细胞的转录组特征分析作为神经退行性疾病治疗开发的模型

Ramaswami, Gokul; Yuva-Aydemir, Yeliz; Akerberg, Brynn; Matthews, Bryan; Williams, Jenna; Golczer, Gabriel; Huang, Jiaqi; Al Abdullatif, Ali; Huh, Dann; Burkly, Linda C; Engle, Sandra J; Grossman, Iris; Sehgal, Alfica; Sigova, Alla A; Fremeau, Robert T Jr; Liu, Yuting; Bumcrot, David

scRNASequest: an ecosystem of scRNA-seq analysis, visualization, and publishing

scRNASequest:一个用于单细胞RNA测序分析、可视化和发表的生态系统

Li, Kejie; Sun, Yu H; Ouyang, Zhengyu; Negi, Soumya; Gao, Zhen; Zhu, Jing; Wang, Wanli; Chen, Yirui; Piya, Sarbottam; Hu, Wenxing; Zavodszky, Maria I; Yalamanchili, Hima; Cao, Shaolong; Gehrke, Andrew; Sheehan, Mark; Huh, Dann; Casey, Fergal; Zhang, Xinmin; Zhang, Baohong

Random partitioning of molecules at cell division

细胞分裂过程中分子的随机分配

Huh, Dann; Paulsson, Johan