In vivo treatment of tyrosinaemia with hypercompact Cas12f1
利用高致密Cas12f1进行酪氨酸血症的体内治疗
期刊:Cell Discovery
影响因子:12.5
doi:10.1038/s41421-023-00554-y
Guo, Ruochen; Li, Zhifang; Li, Guoling; Zhang, Hainan; Zhang, Chang; Huo, Xiaona; Zhang, Xiaoyin; Yang, Xiali; Yang, Rongrong; Liu, Yuanhua; Sun, Xiaozhi; Liu, Xinyu; Yang, Hui; Zhou, Yingsi; Xu, Chunlong