Safety findings from the phase 1/2 MOSAIC study of miransertib for patients with PIK3CA-related overgrowth spectrum or Proteus syndrome
针对PIK3CA相关过度生长谱系或Proteus综合征患者的miransertib 1/2期MOSAIC研究的安全性结果
期刊:Orphanet Journal of Rare Diseases
影响因子:3.5
doi:10.1186/s13023-025-03831-z
Eng, Whitney; Iacobas, Ionela; Perkins, Jonathan; Zampino, Giuseppe; Leoni, Chiara; Buonuomo, Paola Sabrina; Simonetti, Alessandra; Goel, Himanshu; Briones, Michael; Huang, Mo; Goldmacher, Gregory; Liaw, Danny; Hammill, Adrienne