The pyruvate kinase activator mitapivat reduces hemolysis and improves anemia in a β-thalassemia mouse model
丙酮酸激酶激活剂米塔匹伐可减少溶血并改善β-地中海贫血小鼠模型中的贫血。
期刊:Journal of Clinical Investigation
影响因子:13.6
doi:10.1172/JCI144206
Matte, Alessandro; Federti, Enrica; Kung, Charles; Kosinski, Penelope A; Narayanaswamy, Rohini; Russo, Roberta; Federico, Giorgia; Carlomagno, Francesca; Desbats, Maria Andrea; Salviati, Leonardo; Leboeuf, Christophe; Valenti, Maria Teresa; Turrini, Francesco; Janin, Anne; Yu, Shaoxia; Beneduce, Elisabetta; Ronseaux, Sebastien; Iatcenko, Iana; Dang, Lenny; Ganz, Tomas; Jung, Chun-Ling; Iolascon, Achille; Brugnara, Carlo; De Franceschi, Lucia