Platform trial design for neurofibromatosis type 1, NF2-related schwannomatosis and non-NF2-related schwannomatosis: A potential model for rare diseases
针对1型神经纤维瘤病、NF2相关神经鞘瘤病和非NF2相关神经鞘瘤病的平台试验设计:一种潜在的罕见病模型
期刊:Neuro-Oncology Practice
影响因子:2.5
doi:10.1093/nop/npae001
Dhaenens, Britt A E; Heimann, Günter; Bakker, Annette; Nievo, Marco; Ferner, Rosalie E; Evans, D Gareth; Wolkenstein, Pierre; Leubner, Jonas; Potratz, Cornelia; Carton, Charlotte; Iloeje, Uchenna; Kirk, George; Blakeley, Jaishri O; Plotkin, Scott; Fisher, Michael J; Kim, AeRang; Driever, Pablo Hernáiz; Azizi, Amedeo A; Widemann, Brigitte C; Gross, Andrea; Parke, Tom; Legius, Eric; Oostenbrink, Rianne