Overloaded Adeno-Associated Virus as a Novel Gene Therapeutic Tool for Otoferlin-Related Deafness
超载腺相关病毒作为耳聋基因治疗新工具
期刊:Frontiers in Molecular Neuroscience
影响因子:3.5
doi:10.3389/fnmol.2020.600051
Vladan Rankovic, Christian Vogl, Nele M Dörje, Iman Bahader, Carlos J Duque-Afonso, Anupriya Thirumalai, Thomas Weber, Kathrin Kusch, Nicola Strenzke, Tobias Moser