ABE8e adenine base editor precisely and efficiently corrects a recurrent COL7A1 nonsense mutation
ABE8e 腺嘌呤碱基编辑器可精确有效地纠正复发的 COL7A1 无义突变
期刊:Scientific Reports
影响因子:3.8
doi:10.1038/s41598-022-24184-8
Adam Sheriff, Ina Guri, Paulina Zebrowska, Virginia Llopis-Hernandez, Imogen R Brooks, Stavroula Tekkela, Kavita Subramaniam, Ruta Gebrezgabher, Gaetano Naso, Anastasia Petrova, Katarzyna Balon, Alexandros Onoufriadis, Dorota Kujawa, Martyna Kotulska, Gregory Newby, Łukasz Łaczmański, David R Liu, J