Improved bi-allelic modification of a transcriptionally silent locus in patient-derived iPSC by Cas9 nickase
通过 Cas9 切口酶对患者来源的 iPSC 中的转录沉默位点进行改进的双等位基因修饰
期刊:Scientific Reports
影响因子:3.8
doi:10.1038/srep38198
Reto Eggenschwiler, Mohsen Moslem, Mariane Serra Fráguas, Melanie Galla, Oliver Papp, Maximilian Naujock, Ines Fonfara, Ingrid Gensch, Annabell Wähner, Abbas Beh-Pajooh, Claudio Mussolino, Marcel Tauscher, Doris Steinemann, Florian Wegner, Susanne Petri, Axel Schambach, Emmanuelle Charpentier, Toni