Two randomised controlled phase 2 studies of the oral neutrophil elastase inhibitor alvelestat in alpha-1 antitrypsin deficiency
两项随机对照 II 期研究评估了口服中性粒细胞弹性蛋白酶抑制剂阿维司他治疗 α1-抗胰蛋白酶缺乏症的疗效
期刊:European Respiratory Journal
影响因子:21
doi:10.1183/13993003.01019-2025
Wells, J Michael; Titlestad, Ingrid L; Tanash, Hanan; Turner, Alice M; Chapman, Kenneth R; Hatipoğlu, Umur Ş; Goldklang, Monica P; D'Armiento, Jeanine M; Pirozzi, Cheryl S; Drummond, M Bradley; Barjaktarevic, Igor Z; Chatila, Wissam M; Devine, Megan S; Strange, Charlie; Sandhaus, Robert A; Parkin, Jacqueline M; Westfall, Elizabeth; Lin, Vivian Y; Parks, Robin; Kuo, Hui-Chien; Ekue, Adzoa; Moffitt, Kelly L; Inshaw, Jamie; Aban, Inmaculada; Dransfield, Mark T; Stockley, Robert A