Personalized allele-specific antisense oligonucleotides for GNAO1-neurodevelopmental disorder
针对 GNAO1 神经发育障碍的个性化等位基因特异性反义寡核苷酸
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.5
doi:10.1016/j.omtn.2024.102432
Inna Shomer, Nofar Mor, Shaul Raviv, Noga Budick-Harmelin, Tanya Matchevich, Sharon Avkin-Nachum, Yoach Rais, Rebecca Haffner-Krausz, Ariela Haimovich, Aviv Ziv, Reut Fluss, Bruria Ben-Ze'ev, Gali Heimer, Denis N Silachev, Vladimir L Katanaev, Dan Dominissini
