日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Targeting human plasma cells using regulated BCMA CAR T cells eliminates circulating antibodies in humanized mice.

利用调控的BCMA CAR T细胞靶向人类浆细胞,可消除人源化小鼠体内的循环抗体

Honaker Yuchi, Gruber David, Jacobs Chester, Yu-Hong Cheng Rene, Patel Shivani, Galvan Christopher Zavala, Khan Iram F, Zhou Kevin, Sommer Karen, Astrakhan Alexander, Cook Peter J, James Richard G, Rawlings David J

DNA-PK inhibition enhances gene editing efficiency in HSPCs for CRISPR-based treatment of X-linked hyper IgM syndrome.

DNA-PK 抑制剂可提高 HSPC 中基因编辑的效率,从而利用 CRISPR 技术治疗 X 连锁高 IgM 综合征

Pugliano Cole M, Berger Mason, Ray Roslyn M, Sapkos Kai, Wu Betty, Laird Aidan, Ye Yidian, Thomson Daniel, DeGottardi M Quinn, Khan Iram F, Tatiossian Kristina, Miles Brodie A, Aeschimann Florian, Pasquier Jerome, Kim Mihee M, Rawlings David J

Efficient and sustained FOXP3 locus editing in hematopoietic stem cells as a therapeutic approach for IPEX syndrome

高效、持续的造血干细胞 FOXP3 基因座编辑作为 IPEX 综合征的治疗方法

Swati Singh, Cole M Pugliano, Yuchi Honaker, Aidan Laird, M Quinn DeGottardi, Ezra Lopez, Stefan Lachkar, Claire Stoffers, Karen Sommer, Iram F Khan, David J Rawlings

Ex vivo engineered human plasma cells exhibit robust protein secretion and long-term engraftment in vivo

离体工程人类浆细胞表现出强大的蛋白质分泌和体内长期植入

Rene Yu-Hong Cheng, King L Hung, Tingting Zhang, Claire M Stoffers, Andee R Ott, Emmaline R Suchland, Nathan D Camp, Iram F Khan, Swati Singh, Ying-Jen Yang, David J Rawlings, Richard G James2

Single-centre study surveying neurology trainees' and faculty's perceptions of the impact of the COVID-19 pandemic on residents' medical education

一项单中心研究调查了神经内科住院医师和教职人员对新冠疫情对住院医师医学教育影响的看法。

Alhajala, Hisham; Ramadan, Ahmad Riad; Suneja, Aarushi; Schultz, Lonni; Zaman, Iram F

Effective, safe, and sustained correction of murine XLA using a UCOE-BTK promoter-based lentiviral vector

使用基于 UCOE-BTK 启动子的慢病毒载体有效、安全且持续地校正小鼠 XLA

Brenda J Seymour, Swati Singh, Hannah M Certo, Karen Sommer, Blythe D Sather, Socheath Khim, Courtnee Clough, Malika Hale, Joseph Pangallo, Byoung Y Ryu, Iram F Khan, Jennifer E Adair, David J Rawlings

Tales of a department: how the COVID-19 pandemic transformed Detroit's Henry Ford Hospital, Department of Neurology-part I: the surge

科室故事:新冠疫情如何改变底特律亨利·福特医院神经内科——第一部分:激增

Ramadan, Ahmad Riad; Alsrouji, Owais K; Cerghet, Mirela; Chopp, Michael; Danoun, Omar; Grover, Kavita M; Ismail, Mohammed; Katramados, Angelos M; Mohamed, Ghada A; Mehta, Chandan B; Newman, Daniel S; Osman, Gamaleldin; Reuther, Jackie; Sallowm, Yamin; Zaman, Iram F; Barkley, Gregory L

Engineering Protein-Secreting Plasma Cells by Homology-Directed Repair in Primary Human B Cells

通过同源性定向修复在原代人类 B 细胞中改造分泌蛋白质的浆细胞

King L Hung, Iana Meitlis, Malika Hale, Chun-Yu Chen, Swati Singh, Shaun W Jackson, Carol H Miao, Iram F Khan, David J Rawlings, Richard G James

Accelerated epigenetic aging and mitochondrial DNA copy number in bipolar disorder

双相情感障碍患者的表观遗传衰老加速和线粒体 DNA 拷贝数

Gabriel R Fries, Isabelle E Bauer, Giselli Scaini, Mon-Ju Wu, Iram F Kazimi, Samira S Valvassori, Giovana Zunta-Soares, Consuelo Walss-Bass, Jair C Soares, Joao Quevedo

High Efficiency CRISPR/Cas9-mediated Gene Editing in Primary Human T-cells Using Mutant Adenoviral E4orf6/E1b55k "Helper" Proteins

使用突变腺病毒 E4orf6/E1b55k“辅助”蛋白在原代人类 T 细胞中进行高效 CRISPR/Cas9 介导的基因编辑

Kamila S Gwiazda, Alexandra E Grier, Jaya Sahni, Stephen M Burleigh, Unja Martin, Julia G Yang, Nicholas A Popp, Michelle C Krutein, Iram F Khan, Kyle Jacoby, Michael C Jensen, David J Rawlings, Andrew M Scharenberg