Dual-AAV vector-mediated expression of MYO7A improves vestibular function in a mouse model of Usher syndrome 1B
双 AAV 载体介导的 MYO7A 表达可改善 Usher 综合征 1B 小鼠模型的前庭功能
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:
doi:10.1016/j.omtm.2023.08.012
Samantha C Lau, Mhamed Grati, Kevin Isgrig, Moaz Sinan, Kaitlyn R Calabro, Jianliang Zhu, Yasuko Ishibashi, Zeynep Ozgur, Talah Wafa, Inna A Belyantseva, Tracy Fitzgerald, Thomas B Friedman, Sanford L Boye, Shannon E Boye, Wade W Chien