Consensus guidelines for the monitoring and management of metachromatic leukodystrophy in the United States
美国异染性脑白质营养不良症监测和管理共识指南
期刊:Cytotherapy
影响因子:3.2
doi:10.1016/j.jcyt.2024.03.487
Adang, Laura A; Bonkowsky, Joshua L; Boelens, Jaap Jan; Mallack, Eric; Ahrens-Nicklas, Rebecca; Bernat, John A; Bley, Annette; Burton, Barbara; Darling, Alejandra; Eichler, Florian; Eklund, Erik; Emrick, Lisa; Escolar, Maria; Fatemi, Ali; Fraser, Jamie L; Gaviglio, Amy; Keller, Stephanie; Patterson, Marc C; Orchard, Paul; Orthmann-Murphy, Jennifer; Santoro, Jonathan D; Schöls, Ludger; Sevin, Caroline; Srivastava, Isha N; Rajan, Deepa; Rubin, Jennifer P; Van Haren, Keith; Wasserstein, Melissa; Zerem, Ayelet; Fumagalli, Francesca; Laugwitz, Lucia; Vanderver, Adeline