Optimization of HITI-Mediated Gene Insertion for Rhodopsin and Peripherin-2 in Mouse Rod Photoreceptors: Targeting Dominant Retinitis Pigmentosa.
优化 HITI 介导的视紫红质和 Peripherin-2 在小鼠视杆光感受器中的基因插入:靶向显性视网膜色素变性
期刊:Investigative Ophthalmology & Visual Science
影响因子:4.7
doi:10.1167/iovs.65.13.38
Onishi Akishi, Tsunekawa Yuji, Mandai Michiko, Ishimaru Aiko, Ohigashi Yoko, Sho Junki, Yasuda Kazushi, Suzuki Keiichiro, Izpisua Belmonte Juan Carlos, Matsuzaki Fumio, Takahashi Masayo