AAV-mediated gene therapy in the guanylate cyclase (RetGC1/RetGC2) double knockout mouse model of Leber congenital amaurosis
AAV 介导的莱伯先天性黑蒙症鸟苷酸环化酶 (RetGC1/RetGC2) 双敲除小鼠模型基因治疗
期刊:Human Gene Therapy
影响因子:3.9
doi:10.1089/hum.2012.193
Sanford L Boye, Igor V Peshenko, Wei Chieh Huang, Seok Hong Min, Issam McDoom, Christine N Kay, Xuan Liu, Frank M Dyka, Thomas C Foster, Yumiko Umino, Sukanya Karan, Samuel G Jacobson, Wolfgang Baehr, Alexander Dizhoor, William W Hauswirth, Shannon E Boye