日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

AAV-mediated gene therapy in the guanylate cyclase (RetGC1/RetGC2) double knockout mouse model of Leber congenital amaurosis

AAV 介导的莱伯先天性黑蒙症鸟苷酸环化酶 (RetGC1/RetGC2) 双敲除小鼠模型基因治疗

Sanford L Boye, Igor V Peshenko, Wei Chieh Huang, Seok Hong Min, Issam McDoom, Christine N Kay, Xuan Liu, Frank M Dyka, Thomas C Foster, Yumiko Umino, Sukanya Karan, Samuel G Jacobson, Wolfgang Baehr, Alexander Dizhoor, William W Hauswirth, Shannon E Boye