Lessons for future clinical trials in adults with Becker muscular dystrophy: Disease progression detected by muscle magnetic resonance imaging, clinical and patient-reported outcome measures
对未来贝克尔肌营养不良症成人临床试验的启示:通过肌肉磁共振成像、临床和患者报告结局指标检测疾病进展
期刊:European Journal of Neurology
影响因子:3.9
doi:10.1111/ene.16282
De Wel, Bram; Iterbeke, Louise; Huysmans, Lotte; Peeters, Ronald; Goosens, Veerle; Dubuisson, Nicolas; van den Bergh, Peter; Van Parijs, Vinciane; Remiche, Gauthier; De Waele, Liesbeth; Maes, Frederik; Dupont, Patrick; Claeys, Kristl G