Cell-specific delivery of GJB2 restores auditory function in mouse models of DFNB1 deafness and mediates appropriate expression in NHP cochlea
细胞特异性递送GJB2可恢复DFNB1耳聋小鼠模型的听觉功能,并介导其在非人灵长类动物耳蜗中的适当表达。
期刊:Nature Communications
影响因子:15.7
doi:10.1038/s41467-025-66110-2
Ivanchenko, Maryna V; Booth, Kevin T A; Karavitaki, K Domenica; Antonellis, Larisa M; Nagy, M Aurel; Peters, Cole W; Price, Spencer; Li, Yaqiao; Lytvyn, Anton; Ward, Andrew; Griffith, Eric C; Hrvatin, Sinisa; Greenberg, Michael E; Corey, David P