日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

DNA binding and transposition activity of the Sleeping Beauty transposase: role of structural stability of the primary DNA-binding domain

Sleeping Beauty 转座酶的 DNA 结合和转座活性:初级 DNA 结合域结构稳定性的作用

Ranjan, Venkatesh V; Leighton, Gage O; Yan, Chenbo; Arango, Maria; Lustig, Janna; Corona, Rosario I; Guo, Jun-Tao; Nesmelov, Yuri E; Ivics, Zoltán; Nesmelova, Irina V

Generation and GMP scale-up of human CAR-T cells using non-viral Sleeping Beauty transposons for B cell malignances

利用非病毒Sleeping Beauty转座子制备和GMP规模化生产用于治疗B细胞恶性肿瘤的人类CAR-T细胞

Diez, Begoña; Calviño, Cristina; Fernández-García, María; Rodríguez-Márquez, Paula; Rodríguez-Díaz, Saray; Martínez-Turillas, Rebeca; Ceballos, Candela; Illarramendi, Jorge; Serrano-López, Juana; Miskey, Csaba; Navarro-Bailón, Almudena; López-Corral, Lucía; Llamas, Pilar; Redondo, Margarita; Sánchez-Guijo, Fermín; Rifon, Jose; Alfonso-Piérola, Ana; Ivics, Zoltán; Inogés, Susana; López-Díaz de Cerio, Ascensión; Yanez, Rosa; Bueren, Juan A; Rodríguez-Madoz, Juan R; Prosper, Felipe

The best of both worlds: AAV-mediated gene transfer empowered by LNP delivery of Sleeping Beauty transposase for durable transgene expression in vivo

两全其美:利用LNP递送Sleeping Beauty转座酶,通过AAV介导的基因转移实现体内持久的转基因表达。

Sandoval-Villegas, Nicolás; Ivics, Zoltán

Engineering of potent CAR NK cells using non-viral Sleeping Beauty transposition from minimalistic DNA vectors

利用非病毒Sleeping Beauty转座技术,从最小DNA载体构建高效CAR NK细胞

Bexte, Tobias; Botezatu, Lacramioara; Miskey, Csaba; Gierschek, Fenja; Moter, Alina; Wendel, Philipp; Reindl, Lisa Marie; Campe, Julia; Villena-Ossa, Jose Francisco; Gebel, Veronika; Stein, Katja; Cathomen, Toni; Cremer, Anjali; Wels, Winfried S; Hudecek, Michael; Ivics, Zoltán; Ullrich, Evelyn

A novel hyperactive variant of the Sleeping Beauty transposase facilitates non-viral genome engineering.

睡美人转座酶的一种新型高活性变体促进了非病毒基因组工程

Ochmann Matthias Thomas, Miskey Csaba, Botezatu Lacramioara, Sandoval-Villegas Nicolás, Diem Tanja, Ivics Zoltán

Spatiotemporal analysis of SARS-CoV-2 infection reveals an expansive wave of monocyte-derived macrophages associated with vascular damage and virus clearance in hamster lungs

对SARS-CoV-2感染的时空分析揭示了仓鼠肺部血管损伤和病毒清除过程中单核细胞衍生巨噬细胞的大量涌现。

Ola Bagato ,Anne Balkema-Buschmann ,Daniel Todt ,Saskia Weber ,André Gömer ,Bingqian Qu ,Csaba Miskey ,Zoltan Ivics ,Thomas C Mettenleiter ,Stefan Finke ,Richard J P Brown ,Angele Breithaupt ,Dmitry S Ushakov

Downregulation of transposable elements extends lifespan in Caenorhabditis elegans

转座因子的下调延长了秀丽隐杆线虫的寿命

Ádám Sturm, Éva Saskői, Bernadette Hotzi, Anna Tarnóci, János Barna, Ferenc Bodnár, Himani Sharma, Tibor Kovács, Eszter Ari, Nóra Weinhardt, Csaba Kerepesi, András Perczel, Zoltán Ivics, Tibor Vellai

Passer, a highly active transposon from a fish genome, as a potential new robust genetic manipulation tool

Passer是一种来自鱼类基因组的高活性转座子,有望成为一种新型的、强大的基因操作工具。

Wang, Saisai; Gao, Bo; Miskey, Csaba; Guan, Zhongxia; Sang, Yatong; Chen, Cai; Wang, Xiaoyan; Ivics, Zoltán; Song, Chengyi

Accelerating development of engineered T cell therapies in the EU: current regulatory framework for studying multiple product versions and T2EVOLVE recommendations

加速欧盟工程化T细胞疗法的研发:当前研究多种产品版本的监管框架及T2EVOLVE建议

Ammar, Delphine; Schapitz, Inga; Luu, Maik; Hudecek, Michael; Meyer, Miriam; Taps, Timmothy; Schröder, Bernd; Ivics, Zoltán; Sanges, Carmen; Franz, Paul; Koehl, Ulrike; Negre, Helene; Johanna, Inez; Awigena-Cook, Jacquelyn

Anti-CD117 CAR T cells incorporating a safety switch eradicate human acute myeloid leukemia and hematopoietic stem cells

含有安全开关的抗 CD117 CAR-T 细胞可消灭人类急性髓系白血病和造血干细胞

Chiara F Magnani, Renier Myburgh, Silvan Brunn, Morgane Chambovey, Marianna Ponzo, Laura Volta, Francesco Manfredi, Christian Pellegrino, Steve Pascolo, Csaba Miskey, Zoltán Ivics, Judith A Shizuru, Dario Neri, Markus G Manz