Hemophilia A ameliorated in mice by CRISPR-based in vivo genome editing of human Factor VIII
基于 CRISPR 的人类因子 VIII 体内基因组编辑可改善小鼠的血友病 A
期刊:Scientific Reports
影响因子:3.8
doi:10.1038/s41598-019-53198-y
Hainan Chen, Mi Shi, Avital Gilam, Qi Zheng, Yin Zhang, Ivka Afrikanova, Jinling Li, Zoya Gluzman, Ruhong Jiang, Ling-Jie Kong, Ruby Yanru Chen-Tsai