Halting Recombinant Adeno-Associated Virus Transgene Expression Using mRNA-Lipid Nanoparticle-Delivered Meganucleases.
利用mRNA-脂质纳米颗粒递送的巨核酸酶抑制重组腺相关病毒转基因表达
期刊:Human Gene Therapy
影响因子:4
doi:10.1089/hum.2025.011
Tavora Rubens, Zhang Lizhou, Tran Mai H, Li Hao, O'Hagan Dan, Pan Andi, Barrett Lorenzo, Jablonski Joseph A, Mediouni Sonia, Lopez Alexander, Comella Zachary, Bailey Charles, Choe Hyeryun, Farzan Michael, Valente Susana T
