Adeno-associated vector corneal gene therapy reverses corneal clouding in a feline model of mucopolysaccharidosis VI
腺相关载体角膜基因疗法逆转了猫粘多糖贮积症VI型模型中的角膜混浊
期刊:PLoS One
影响因子:2.6
doi:10.1371/journal.pone.0338370
Gilger, Brian C; Song, Liujiang; Hasegawa, Tomoko; Salmon, Jacklyn H; Bower, Jacquelyn J; Vridhachalam, Naveen; Collins, Elisabeth; Roberts, Darby; Bagel, Jessica; Molony, Caitlyn; Vite, Charles; Hirsch, Matthew L