Preclinical evaluation for engraftment of CD34+ cells gene-edited at the sickle cell disease locus in xenograft mouse and non-human primate models
在异种移植小鼠和非人类灵长类动物模型中对镰状细胞病基因座进行基因编辑的 CD34+ 细胞植入的临床前评估
期刊:Cell Reports Medicine
影响因子:11.7
doi:10.1016/j.xcrm.2021.100247
Naoya Uchida, Linhong Li, Tina Nassehi, Claire M Drysdale, Morgan Yapundich, Jackson Gamer, Juan J Haro-Mora, Selami Demirci, Alexis Leonard, Aylin C Bonifacino, Allen E Krouse, N Seth Linde, Cornell Allen, Madhusudan V Peshwa, Suk See De Ravin, Robert E Donahue, Harry L Malech, John F Tisdale