Customized antisense oligonucleotide-based therapy for neurofilament-associated Charcot-Marie-Tooth disease.
针对神经丝相关夏科-马里-图斯病的定制化反义寡核苷酸疗法
期刊:Brain
影响因子:11.7
doi:10.1093/brain/awae225
Medina Jessica, Rebelo Adriana, Danzi Matt C, Jacobs Elizabeth H, Xu Isaac R L, Ahrens Kathleen P, Chen Sitong, Raposo Jacquelyn, Yanick Christopher, Zuchner Stephan, Saporta Mario A
