Clinical Trial Landscape of Gene-Edited Autologous Hematopoietic Stem Cells for Hemoglobinopathies and Immunodeficiencies
基因编辑自体造血干细胞治疗血红蛋白病和免疫缺陷的临床试验概况
期刊:Oncologist
影响因子:4.2
doi:10.1093/oncolo/oyag110
Mackler, Emily R; Norman, Siobhan; Jalloul-Rizk, Farah; O’Hanlon Cohrt, Karen; O’Dea, Shirley