Randomized double-blind placebo-controlled crossover trial with pyridostigmine in spinal muscular atrophy types 2-4
吡啶斯的明治疗脊髓性肌萎缩症2-4型的随机双盲安慰剂对照交叉试验
期刊:Brain Communications
影响因子:4.5
doi:10.1093/braincomms/fcac324
Stam, Marloes; Wijngaarde, Camiel A; Bartels, Bart; Asselman, Fay-Lynn; Otto, Louise A M; Habets, Laura E; van Eijk, Ruben P A; Middelkoop, Bas M; Goedee, H Stephan; de Groot, Janke F; Roes, Kit C B; Schoenmakers, Marja A G C; Nieuwenhuis, Edward E S; Cuppen, Inge; van den Berg, Leonard H; Wadman, Renske I; van der Pol, W Ludo