Directed evolution of liver-detargeted AAV vectors for systemic gene delivery to skeletal muscle and heart
定向进化肝脏去靶向AAV载体,用于将基因系统性递送至骨骼肌和心脏
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2025.101571
Firnberg, Elad; Tejada, Sigmund K S; Yost, Samantha A; Giles, April R; Choi, Heonhwa; Foltz, Steven J; Qian, Randolph; Smith, Jared B; Heithoff, Benjamin; Elliott, Kirk; David Hou, Chun-Feng; Bernstein, Ashley D; Karumuthil-Melethil, Subha; Chen, Victor Shugui; Mayer, Ayda; Mercer, Andrew C; Kaelber, Jason T; Liu, Ye; Danos, Olivier