Patisiran Treatment in Patients with Transthyretin Cardiac Amyloidosis
帕替西兰治疗转甲状腺素蛋白心脏淀粉样变性患者
期刊:New England Journal of Medicine
影响因子:78.5
doi:10.1056/NEJMoa2300757
Maurer, Mathew S; Kale, Parag; Fontana, Marianna; Berk, John L; Grogan, Martha; Gustafsson, Finn; Hung, Rebecca R; Gottlieb, Robert L; Damy, Thibaud; González-Duarte, Alejandra; Sarswat, Nitasha; Sekijima, Yoshiki; Tahara, Nobuhiro; Taylor, Mark S; Kubanek, Milos; Donal, Erwan; Palecek, Tomas; Tsujita, Kenichi; Tang, W H Wilson; Yu, Wen-Chung; Obici, Laura; Simões, Marcus; Fernandes, Fábio; Poulsen, Steen Hvitfeldt; Diemberger, Igor; Perfetto, Federico; Solomon, Scott D; Di Carli, Marcelo; Badri, Prajakta; White, Matthew T; Chen, Jihong; Yureneva, Elena; Sweetser, Marianne T; Jay, Patrick Y; Garg, Pushkal P; Vest, John; Gillmore, Julian D