日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Effects of vutrisiran on cardiac structure and function in patients with transthyretin amyloidosis with cardiomyopathy: secondary outcomes of the HELIOS-B trial

伏特里西兰对伴有心肌病的转甲状腺素蛋白淀粉样变性患者心脏结构和功能的影响:HELIOS-B试验的次要终点

Jering, Karola S; Fontana, Marianna; Lairez, Olivier; Longhi, Simone; Azevedo, Olga; Morbach, Caroline; Bender, Shaun; Jay, Patrick Y; Vest, John; Bulwer, Bernard E; Prasad, Narayana; Solomon, Scott D; Skali, Hicham

Five-Year Results With Patisiran for Hereditary Transthyretin Amyloidosis With Polyneuropathy: A Randomized Clinical Trial With Open-Label Extension

帕替西兰治疗伴有多发性神经病变的遗传性转甲状腺素蛋白淀粉样变性五年结果:一项开放标签扩展的随机临床试验

Adams, David; Wixner, Jonas; Polydefkis, Michael; Berk, John L; Conceição, Isabel M; Dispenzieri, Angela; Peltier, Amanda; Ueda, Mitsuharu; Bender, Shaun; Capocelli, Kelley; Jay, Patrick Y; Yureneva, Elena; Obici, Laura

Modeling potential cost-effectiveness of tirzepatide versus lifestyle modification for patients with overweight and obesity

对超重和肥胖患者,采用替泽帕肽与生活方式干预相比,进行潜在成本效益建模分析

Hoog, Meredith M; Kan, Hong; Deger, Kristen A; Sorensen, Sonja; Neff, Lisa M; Bae, Jay Patrick; Hankosky, Emily Ruth; Murphy, Madhumita; Mojdami, Donna; Houisse, Ivan; Harris, Mack S

Impact of patisiran on polyneuropathy of hereditary transthyretin amyloidosis in patients with a V122I or T60A variant: a phase IV multicenter study

帕替西兰对携带 V122I 或 T60A 变异的遗传性转甲状腺素蛋白淀粉样变性患者多发性神经病的影响:一项 IV 期多中心研究

Hussain, Yessar; Malhotra, Saurabh; Sperry, Brett W; Shu, Francy; Ananthasubramaniam, Karthikeyan; Desai, Urvi; Egolum, Ugochukwu; Fernandez, Joel; Freimer, Miriam; Mauricio, Elizabeth; Quan, Dianna; Small, Roy; Capocelli, Kelley; Roblin, Steven; Bender, Shaun; Jay, Patrick Y; Yureneva, Elena; Zolty, Ronald

Patisiran Treatment in the Brazilian Subpopulation of the Phase 3 APOLLO-B Study in Transthyretin Amyloidosis with Cardiomyopathy: Post Hoc Analysis

在转甲状腺素蛋白淀粉样变性合并心肌病患者中,巴西亚组人群接受帕替西兰治疗的3期APOLLO-B研究:事后分析

Mesquita, Claudio Tinoco; Schwartzmann, Pedro; Correia, Edileide Barros; Simões, Marcus V; Biolo, Andreia; Duque, Daniel Rodriguez; Jay, Patrick Y; Fernandes, Fábio

Benefits of Patisiran on Functional Capacity in ATTR Cardiac Amyloidosis: Post Hoc Analysis of APOLLO-B

帕替西兰对 ATTR 型心脏淀粉样变性患者功能能力的影响:APOLLO-B 研究的事后分析

Berk, John L; Lairez, Olivier; Schwartzmann, Pedro; Bender, Shaun; White, Matthew T; Jay, Patrick Y; Danese, David; Witteles, Ronald

Patisiran Treatment in Patients with Transthyretin Cardiac Amyloidosis

帕替西兰治疗转甲状腺素蛋白心脏淀粉样变性患者

Maurer, Mathew S; Kale, Parag; Fontana, Marianna; Berk, John L; Grogan, Martha; Gustafsson, Finn; Hung, Rebecca R; Gottlieb, Robert L; Damy, Thibaud; González-Duarte, Alejandra; Sarswat, Nitasha; Sekijima, Yoshiki; Tahara, Nobuhiro; Taylor, Mark S; Kubanek, Milos; Donal, Erwan; Palecek, Tomas; Tsujita, Kenichi; Tang, W H Wilson; Yu, Wen-Chung; Obici, Laura; Simões, Marcus; Fernandes, Fábio; Poulsen, Steen Hvitfeldt; Diemberger, Igor; Perfetto, Federico; Solomon, Scott D; Di Carli, Marcelo; Badri, Prajakta; White, Matthew T; Chen, Jihong; Yureneva, Elena; Sweetser, Marianne T; Jay, Patrick Y; Garg, Pushkal P; Vest, John; Gillmore, Julian D

Heterogeneous cardiac sympathetic innervation gradients promote arrhythmogenesis in murine dilated cardiomyopathy

异质性心脏交感神经支配梯度促进小鼠扩张型心肌病的心律失常发生

Dajani, Al-Hassan J; Liu, Michael B; Olaopa, Michael A; Cao, Lucian; Valenzuela-Ripoll, Carla; Davis, Timothy J; Poston, Megan D; Smith, Elizabeth H; Contreras, Jaime; Pennino, Marissa; Waldmann, Christopher M; Hoover, Donald B; Lee, Jason T; Jay, Patrick Y; Javaheri, Ali; Slavik, Roger; Qu, Zhilin; Ajijola, Olujimi A

Repurposing Normal Chromosomal Microarray Data to Harbor Genetic Insights into Congenital Heart Disease

利用正常染色体微阵列数据揭示先天性心脏病的遗传学信息

Walton, Nephi A; Nguyen, Hoang H; Procknow, Sara S; Johnson, Darren; Anzelmi, Alexander; Jay, Patrick Y

Patisiran treatment in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy after liver transplantation

帕替西兰治疗肝移植后伴有多发性神经病变的遗传性转甲状腺素蛋白介导的淀粉样变性患者

Schmidt, Hartmut H; Wixner, Jonas; Planté-Bordeneuve, Violaine; Muñoz-Beamud, Francisco; Lladó, Laura; Gillmore, Julian D; Mazzeo, Anna; Li, Xingyu; Arum, Seth; Jay, Patrick Y; Adams, David