Sphingolipid-neutralizing molecular therapy reduces psychosine cytotoxicity in Krabbe disease
鞘脂中和分子疗法可降低克拉伯病中精神苷脂的细胞毒性
期刊:iScience
影响因子:4.1
doi:10.1016/j.isci.2026.114808
Begum, Salma; Hsueh, Shin-Chang; Cheria, Ezra M Y; Espejo, Jayar; Zhang, Ping; Collin, Armand; Kappauf, Edgar; Mardenli, Murielle; Gelb, Michael H; Ling, Chang-Chun; Maegawa, Gustavo H B