日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

AAV2 vector optimization for retinal ganglion cell-targeted delivery of therapeutic genes

AAV2 载体优化用于视网膜神经节细胞靶向递送治疗基因

Brahim Chaqour, Thu T Duong, Jipeng Yue, Tehui Liu, David Camacho, Kimberly E Dine, Julian Esteve-Rudd, Scott Ellis, Jean Bennett, Kenneth S Shindler, Ahmara G Ross

CRISPR-Cas9 correction of a nonsense mutation in LCA5 rescues lebercilin expression and localization in human retinal organoids

CRISPR-Cas9 校正 LCA5 中的无义突变可挽救人类视网膜类器官中 lebercilin 的表达和定位

Tess A V Afanasyeva, Dimitra Athanasiou, Pedro R L Perdigao, Kae R Whiting, Lonneke Duijkers, Galuh D N Astuti, Jean Bennett, Alejandro Garanto, Jacqueline van der Spuy, Ronald Roepman, Michael E Cheetham, Rob W J Collin

Restoration of Vision and Retinal Responses After Adeno-Associated Virus-Mediated Optogenetic Therapy in Blind Dogs

腺相关病毒介导的光遗传学治疗使盲犬视力和视网膜反应恢复

Sergei Nikonov, Puya Aravand, Arkady Lyubarsky, Roman Nikonov, Angela J Luo, Zhangyong Wei, Albert M Maguire, Nicholas T Phelps, Ivan Shpylchak, Keirnan Willett, Tomas S Aleman, Rachel M Huckfeldt, Pavitra S Ramachandran, Jean Bennett

AAV8BP2 and AAV8 transduce the mammalian cochlear lateral wall and endolymphatic sac with high efficiency

AAV8BP2 和 AAV8 高效传导哺乳动物耳蜗侧壁和内淋巴囊

Kevin Isgrig, Yasuko Ishibashi, Hyun Jae Lee, Jianliang Zhu, Mhamed Grati, Jean Bennett, Andrew J Griffith, Isabelle Roux, Wade W Chien

Refining surgical techniques for efficient posterior semicircular canal gene delivery in the adult mammalian inner ear with minimal hearing loss

改进手术技术,在成年哺乳动物内耳中有效传递后半规管基因,同时最大程度减少听力损失

Jianliang Zhu #, Jin Woong Choi #, Yasuko Ishibashi, Kevin Isgrig, Mhamed Grati, Jean Bennett, Wade Chien

AAV-mediated PEX1 gene augmentation improves visual function in the PEX1-Gly844Asp mouse model for mild Zellweger spectrum disorder

AAV 介导的 PEX1 基因增强可改善轻度 Zellweger 谱系障碍的 PEX1-Gly844Asp 小鼠模型中的视觉功能

Catherine Argyriou, Anna Polosa, Ji Yun Song, Samy Omri, Bradford Steele, Bruno Cécyre, Devin S McDougald, Erminia Di Pietro, Jean-François Bouchard, Jean Bennett, Joseph G Hacia, Pierre Lachapelle, Nancy E Braverman

Treatment Potential for LCA5-Associated Leber Congenital Amaurosis

LCA5 相关莱伯先天性黑蒙的治疗潜力

Katherine E Uyhazi, Puya Aravand, Brent A Bell, Zhangyong Wei, Lanfranco Leo, Leona W Serrano, Denise J Pearson, Ivan Shpylchak, Jennifer Pham, Vidyullatha Vasireddy, Jean Bennett, Tomas S Aleman

RNA Splicing Factor Mutations That Cause Retinitis Pigmentosa Result in Circadian Dysregulation

导致视网膜色素变性的 RNA 剪接因子突变导致昼夜节律失调

Iryna Shakhmantsir, Scott J Dooley, Siddharth Kishore, Dechun Chen, Eric Pierce, Jean Bennett, Amita Sehgal

Drug resistance after cessation of efavirenz-based antiretroviral treatment started in pregnancy

妊娠期开始的以依非韦伦为基础的抗逆转录病毒治疗停药后出现耐药性

Ajibola, Globahan; Rowley, Christopher; Maruapula, Dorcas; Leidner, Jean; Bennett, Kara; Powis, Kathleen; Shapiro, Roger L; Lockman, Shahin

AAV2.7m8 is a powerful viral vector for inner ear gene therapy

AAV2.7m8 是一种用于内耳基因治疗的强大病毒载体

Kevin Isgrig, Devin S McDougald, Jianliang Zhu, Hong Jun Wang, Jean Bennett, Wade W Chien