日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Characterization of residual microRNAs in AAV vector batches produced in HEK293 mammalian cells and Sf9 insect cells

对在HEK293哺乳动物细胞和Sf9昆虫细胞中产生的AAV载体批次中残留的microRNA进行表征

Penaud-Budloo, Magalie; Lecomte, Emilie; Lecomte, Quentin; Pacouret, Simon; Broucque, Frédéric; Guy-Duché, Aurélien; Dupont, Jean-Baptiste; Jeanson-Leh, Laurence; Robin, Cécile; Blouin, Véronique; Ayuso, Eduard; Adjali, Oumeya

miR-708-5p and miR-34c-5p are involved in nNOS regulation in dystrophic context

miR-708-5p 和 miR-34c-5p 参与营养不良症中的 nNOS 调控

Marine Guilbaud, Christel Gentil, Cécile Peccate, Elena Gargaun, Isabelle Holtzmann, Carole Gruszczynski, Sestina Falcone, Kamel Mamchaoui, Rabah Ben Yaou, France Leturcq, Laurence Jeanson-Leh, France Piétri-Rouxel

Circulating miRNAs are generic and versatile therapeutic monitoring biomarkers in muscular dystrophies

循环miRNA是肌营养不良症中通用且用途广泛的治疗监测生物标志物。

Israeli, David; Poupiot, Jérôme; Amor, Fatima; Charton, Karine; Lostal, William; Jeanson-Leh, Laurence; Richard, Isabelle

Short-lived recombinant adeno-associated virus transgene expression in dystrophic muscle is associated with oxidative damage to transgene mRNA

营养不良肌肉中短寿命重组腺相关病毒转基因表达与转基因 mRNA 的氧化损伤有关

Jean-Baptiste Dupont, Benoit Tournaire, Christophe Georger, Béatrice Marolleau, Laurence Jeanson-Leh, Mireille Ledevin, Pierre Lindenbaum, Emilie Lecomte, Benjamin Cogné, Laurence Dubreil, Thibaut Larcher, Bernard Gjata, Laetitia Van Wittenberghe, Caroline Le Guiner, Magalie Penaud-Budloo, Richard O

Determination of anti-adeno-associated virus vector neutralizing antibody titer with an in vitro reporter system

体外报告系统测定抗腺相关病毒载体中和抗体滴度

Amine Meliani, Christian Leborgne, Sabrina Triffault, Laurence Jeanson-Leh, Philippe Veron, Federico Mingozzi

Ku80 participates in the targeting of retroviral transgenes to the chromatin of CHO cells

Ku80参与将逆转录病毒转基因靶向CHO细胞的染色质。

Masson, Christel; Bury-Moné, Stéphanie; Guiot, Elvire; Saez-Cirion, Asier; Schoëvaërt-Brossault, Damien; Brachet-Ducos, Corinne; Delelis, Olivier; Subra, Frédéric; Jeanson-Leh, Laurence; Mouscadet, Jean-François