Rational design and applications of piperazine and cyclohexane ionizable lipids for PKU and SSADH deficiency
哌嗪和环己烷可电离脂质的合理设计及其在苯丙酮尿症和SSADH缺乏症中的应用
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.1
doi:10.1016/j.omtn.2025.102697
Son, Jiyeon; Yoo, Hyunjung; Park, Joonyoung; Park, Hyelim; Chong, Seung-Eun; Lee, Jungeun; Kim, Jeewon; Park, Eunyoung; Bae, Seo-Hyeon; Kang, Sunhee; Ban, Jaeyoung; Song, Soonhwa; Oh, Eunhye; Kwak, Heechun; Kwon, Hyokyoung; Jung, Jaesung; Lee, Narae; Jung, Byunghoon; Zhang, Yuebao; Kang, Diana D; Du, Shi; Shin, Young Kee; Dong, Yizhou; Jeong, Jae Uk