Iduronate-2-sulfatase transport vehicle rescues behavioral and skeletal phenotypes in a mouse model of Hunter syndrome
艾杜糖醛酸-2-硫酸酯酶转运载体挽救亨特综合征小鼠模型中的行为和骨骼表型
期刊:JCI Insight
影响因子:6.3
doi:10.1172/jci.insight.145445
Annie Arguello, René Meisner, Elliot R Thomsen, Hoang N Nguyen, Ritesh Ravi, Jeffrey Simms, Iris Lo, Jessica Speckart, Julia Holtzman, Thomas M Gill, Darren Chan, Yuhsiang Cheng, Chi-Lu Chiu, Jason C Dugas, Meng Fang, Isabel A Lopez, Hilda Solanoy, Buyankhishig Tsogtbaatar, Yuda Zhu, Akhil Bhalla, K