日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A CAG repeat threshold for therapeutics targeting somatic instability in Huntington's disease

针对亨廷顿氏病躯体不稳定性治疗的 CAG 重复阈值

Sarah G Aldous, Edward J Smith, Christian Landles, Georgina F Osborne, Maria Cañibano-Pico, Iulia M Nita, Jemima Phillips, Yongwei Zhang, Bo Jin, Marissa B Hirst, Caroline L Benn, Brian C Bond, Winfried Edelmann, Jonathan R Greene, Gillian P Bates

Alternative processing of human HTT mRNA with implications for Huntington's disease therapeutics

人类 HTT mRNA 的替代加工对亨廷顿氏病治疗具有重要意义

Sandra Fienko, Christian Landles, Kirupa Sathasivam, Sean J McAteer, Rebecca E Milton, Georgina F Osborne, Edward J Smith, Samuel T Jones, Marie K Bondulich, Emily C E Danby, Jemima Phillips, Bridget A Taxy, Holly B Kordasiewicz, Gillian P Bates