AAV9-mediated FIG4 delivery prolongs life span in Charcot-Marie-Tooth disease type 4J mouse model
AAV9 介导的 FIG4 递送可延长 Charcot-Marie-Tooth 病 4J 型小鼠模型的寿命
期刊:Journal of Clinical Investigation
影响因子:13.3
doi:10.1172/JCI137159
Maximiliano Presa, Rachel M Bailey, Crystal Davis, Tara Murphy, Jenn Cook, Randy Walls, Hannah Wilpan, Laurent Bogdanik, Guy M Lenk, Robert W Burgess, Steven J Gray, Cathleen Lutz