日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Repurposing nuclear receptors for ligand-responsive liquid condensate formation and gene regulation

利用核受体调控配体响应性液态凝聚体的形成和基因表达

Rihtar, Erik; Fink, Tina; Ivanovski, Filip; Koplan, Eva; Jerala, Roman

Self-assembling protein cages: from coiled-coil module to machine learning-driven de novo design of next-generation biomaterials

自组装蛋白质笼:从卷曲螺旋模块到机器学习驱动的下一代生物材料的从头设计

Gupta, Arvind Kumar; Esih, Hana; Gradišar, Helena; Jerala, Roman

Beyond Dimerization: Harnessing Tetrameric Coiled-Coils for Nanostructure Assembly

超越二聚化:利用四聚体螺旋卷曲结构组装纳米结构

Vidmar, Sara; Šmidlehner, Tamara; Aupič, Jana; Strmšek, Žiga; Ljubetič, Ajasja; Xiao, Fei; Hu, Guang; Liu, Chuan; Beck, Florian; Erdmann, Philipp S; Jerala, Roman

Programmable Protein-DNA Composite Nanostructures: from Nanostructure Construction to Protein-Induced Micro-Scale Material Self-Assembly and Functionalization

可编程蛋白质-DNA复合纳米结构:从纳米结构构建到蛋白质诱导的微尺度材料自组装和功能化

Zhou, Weijun; Strmšek, Žiga; Snoj, Jaka; Škarabot, Miha; Jerala, Roman

RNA trans-splicing to rescue β-catenin: A novel approach for treating CTNNB1-Haploinsufficiency disorder.

RNA 反式剪接拯救 β-catenin:治疗 CTNNB1 单倍体不足症的新方法

Maruna Matea, Sušjan-Leite Petra, Meško Maja, Miroševič Špela, Jerala Roman

Engineering chimeric PCSK9 for a vaccine against atherosclerosis.

构建嵌合型PCSK9用于抗动脉粥样硬化疫苗

Malenšek Špela, Lainšček Duško, Esih Hana, Orehek Sara, Fink Tina, Urbanc Anja Golob, Blinc Aleš, Jerala Roman

CTGCT, Centre of Excellence for the Technologies of Gene and Cell Therapy: Collaborative translation of scientific discoveries into advanced treatments for neurological rare genetic diseases and cancer

CTGCT,基因与细胞治疗技术卓越中心:致力于将科学发现转化为治疗神经系统罕见遗传疾病和癌症的先进疗法。

Marolt Presen, Darja; Lainšček, Duško; Kinghorn, Jane; Sebestyen, Zsolt; Kuball, Jurgen; Amini, Leila; Reinke, Petra; Fuchs, Anke; Jerala, Roman; Benčina, Mojca

Genotypic, functional, and phenotypic characterization in CTNNB1 neurodevelopmental syndrome.

CTNNB1神经发育综合征的基因型、功能和表型特征

Žakelj Nina, Gosar David, Miroševič Špela, Sanders Stephan J, Ljungdahl Alicia, Kohani Sayeh, Huang Shouhe, Leong Lok I, An Ying, Teo Miou-Jing, Moultrie Fiona, Jerala Roman, Lainšček Duško, Forstnerič Vida, Sušjan Petra, Lisowski Leszek, Perez-Iturralde Andrea, Mrak Jasna Oražem, Chan Ho Yin Edwin, Osredkar Damjan

Gene therapy of rare diseases as a milestone in medicine - overview of the field and report on initial experiences in Slovenia

罕见病基因疗法:医学发展史上的一个里程碑——该领域概述及斯洛文尼亚初步经验报告

Grošelj, Urh; Kavčič, Marko; Drole Torkar, Ana; Kafol, Jan; Lainšček, Duško; Jerala, Roman; Sever, Matjaž; Zver, Samo; Serša, Gregor; Čemažar, Maja; Strojan, Primož; Grošelj, Aleš; Žerjav Tanšek, Mojca; Miroševič, Špela; Ivančan, Simona; Prelog, Tomaž; Gosar, David; Oražem Mrak, Jasna; Mlinarič, Matej; Bertok, Sara; Kovač, Jernej; Kodrič, Jana; Battelino, Saba; Pokorn, Marko; Ihan, Alojz; Jazbec, Janez; Battelino, Tadej; Osredkar, Damjan

Paving the way toward treatment solutions for CTNNB1 syndrome: a patient organization perspective

为CTNNB1综合征的治疗方案铺平道路:患者组织的视角

Miroševič, Špela; Khandelwal, Shivang; Amerson, Emily; Parks, Effie; Parks, Mariana; Cochran, Lauren; González Hernández, Ana; Ferraro, Mirela; Lisowski, Leszek; Perez-Iturralde, Andrea; Chung, Wendy; Jacob, Michele H; Žakelj, Nina; Lainšček, Duško; Forstnerič, Vida; Sušjan, Petra; Maruna, Matea; Jerala, Roman; Osredkar, Damjan